An Expert Overview on Therapies in Non-Transfusion-Dependent Thalassemia: Classical to Cutting Edge in Treatment
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关键词
beta-Thalassemia intermedia(beta-TI)novelpharmacological drugsgene editingclusteredregularly interspaced shortpalindromic repeats(CRISPR)/cas9LIVER IRON CONCENTRATIONBETA-THALASSEMIAEXTRAMEDULLARY HEMATOPOIESISINEFFECTIVE ERYTHROPOIESISLIGAND TRAPMOLECULAR CHARACTERIZATIONCELL TRANSPLANTATIONHEMOGLOBIN-DD-PUNJABINTERMEDIA
发布时间
2024-04-07
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