作者:
Finkel, Richard S. [1]
;
Darras, Basil T. [2]
;
Mendell, Jerry R. [3]
;
Day, John W. [4]
;
Kuntz, Nancy L. [5]
;
Connolly, Anne M. [6]
;
Zaidman, Craig M. [7]
;
Crawford, Thomas O. [8]
;
Butterfield, Russell J. [9]
;
Shieh, Perry B. [10]
;
Tennekoon, Gihan [11]
;
Brandsema, John F. [12]
;
Iannaccone, Susan T. ;
Shoffner, John ;
Kavanagh, Sarah ;
Macek, Thomas A. ;
Tauscher-Wisniewski, Sitra
作者单位:
St Jude Children's Research Hospital,St Jude Childrens Res Hosp
[1]
Dept Neurol,Boston Childrens Hosp
[2]
Ctr Gene Therapy,Nationwide Childrens Hosp
[3]
Dept Neurol,Stanford Univ
[4]
Div Neurol,Ann & Robert H Lurie Childrens Hosp Chicago
[5]
Sch Med,Washington Univ
[6]
Dept Neurol,Johns Hopkins Univ
[7]
Dept Pediat,Univ Utah Hlth
[8]
David Geffen Sch Med,UCLA
[9]
Div Neurol,Childrens Hosp Philadelphia
[10]
Dept Pediat,Univ Texas Southwestern Med Ctr Dallas
[11]
Novartis Gene Therapies Inc
[12]
发布时间
2023-10-21