首页>Molecular genetics and metabolism>RESTORATION OF HEPATIC GALACTOSE-1 PHOSPHATE URIDYLYLTRANSFERASE (GALT) ACTIVITY BY A NOVEL MRNA-BASED THERAPY DECREASES HEPATIC AND RED BLOOD CELL GAL-1P AND PLASMA GALACTOSE
RESTORATION OF HEPATIC GALACTOSE-1 PHOSPHATE URIDYLYLTRANSFERASE (GALT) ACTIVITY BY A NOVEL MRNA-BASED THERAPY DECREASES HEPATIC AND RED BLOOD CELL GAL-1P AND PLASMA GALACTOSE