Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class dissociative steroidal anti-inflammatory drug
作者:
Conklin, Laurie S. [1]
;
Damsker, Jesse M. [2]
;
Hoffman, Eric P. [3]
;
Jusko, William J. [4]
;
Mavroudis, Panteleimon D. [5]
;
Schwartz, Benjamin D. [6]
;
Mengle-Gaw, Laurel J. [7]
;
Smith, Edward C. [8]
;
Mah, Jean K. [9]
;
Guglieri, Michela [10]
;
Nevo, Yoram [11]
;
Kuntz, Nancy [12]
;
McDonald, Craig M. [13]
;
Tulinius, Mar [14]
;
Ryan, Monique M. [15]
;
Webster, Richard [16]
;
Castro, Diana [17]
;
Finkel, Richard S. [18]
;
Smith, Andrea L. [19]
;
Morgenroth, Lauren P. ;
Arrieta, Adrienne ;
Shimony, Maya ;
Jaros, Mark ;
Shale, Phil ;
McCall, John M. ;
Hathout, Yetrib ;
Nagaraju, Kanneboyina ;
van den Anker, John ;
Ward, Leanne M. ;
Ahmet, Alexandra ;
Cornish, Michaelyn R. ;
Clemens, Paula R.
作者单位:
Newcastle Univ, Newcastle Upon Tyne, Tyne & Wear, England
[1]
ReveraGen Biopharma LLC, Rockville, MD USA
[2]
Childrens Hosp Eastern Ontario, Ottawa, ON, Canada
[3]
Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL 60611 USA
[4]
Univ Calif Davis, Davis, CA 95616 USA
[5]
Queen Silvia Childrens Hosp, Gothenburg, Sweden
[6]
Univ Melbourne, Royal Childrens Hosp, Melbourne, Vic, Australia
[7]
Camden Grp LLC, St Louis, MO USA
[8]
SUNY Buffalo, Buffalo, NY USA
[9]
Univ Texas Southwestern, Dallas, TX USA
[10]
TRiNDS LLC, Kensington, MD USA
[11]
Duke Univ, Durham, NC USA
[12]
Univ Calgary, Alberta Childrens Hosp, Calgary, AB, Canada
[13]
Univ Pittsburgh, Pittsburgh, PA USA
[14]
Nemours Childrens Hosp, Orlando, FL USA
[15]
Summit Analyt, Denver, CO USA
[16]
Tel Aviv Univ, Schneider Childrens Med Ctr Israel, Tel Aviv, Israel
[17]
Childrens Hosp Westmead, Sydney, NSW, Australia
[18]
SUNY Binghamton, Binghamton, NY USA
[19]
发布时间
2019-05-25
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Pharmacological research
Pharmacological research
140-150页
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