换一批Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access
第一作者：
Fumagalli, Francesca
作者：
Fumagalli, Francesca [1]
;
Calbi, Valeria [2]
;
Sora, Maria Grazia Natali [3]
;
Sessa, Maria [4]
;
Baldoli, Cristina [5]
;
Rancoita, Paola Maria, V [6]
;
Ciotti, Francesca [7]
;
Sarzana, Marina [8]
;
Fraschini, Maddalena [9]
;
Zambon, Alberto Andrea [10]
;
Acquati, Serena ;
Redaelli, Daniela ;
Attanasio, Vanessa ;
Miglietta, Simona ;
De Mattia, Fabiola ;
Barzaghi, Federica ;
Ferrua, Francesca ;
Migliavacca, Maddalena ;
Tucci, Francesca ;
Gallo, Vera ;
Del Carro, Ubaldo ;
Canale, Sabrina ;
Spiga, Ivana ;
Lorioli, Laura ;
Recupero, Salvatore ;
Fratini, Elena Sophia ;
Morena, Francesco ;
Silvani, Paolo ;
Calvi, Maria Rosa ;
Facchini, Marcella ;
Locatelli, Sara ;
Corti, Ambra ;
Zancan, Stefano ;
Antonioli, Gigliola ;
Farinelli, Giada ;
Gabaldo, Michela ;
Garcia-Segovia, Jesus ;
Schwab, Laetitia C. ;
Downey, Gerald F. ;
Filippi, Massimo ;
Cicalese, Maria Pia ;
Martino, Sabata ;
Di Serio, Clelia ;
Ciceri, Fabio ;
Bernardo, Maria Ester ;
Naldini, Luigi ;
Biffi, Alessandra ;
Aiuti, Alessandro
作者单位：
Unit Neurol,IRCCS San Raffaele Sci Inst
[1]
San Raffaele Telethon Inst Gene Therapy SR Tiget,IRCCS San Raffaele Sci Inst
[2]
Dept Chem Biol & Biotechnol,Univ Perugia
[3]
Univ Ctr Stat Biomed Sci CUSSB
[4]
Unit Hematol & Bone Marrow Transplantat,IRCCS San Raffaele Sci Inst
[5]
Neuroradiol Unit,IRCCS San Raffaele Sci Inst
[6]
Pediat Immunohematol Unit,IRCCS San Raffaele Sci Inst
[7]
Clin Mol Biol Lab,IRCCS San Raffaele Sci Inst
[8]
Dept Anesthesia & Crit Care,IRCCS San Raffaele Sci Inst
[9]
OrchardTherapeut Europe
[10]
发布时间
2022-07-13
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