Once-daily, subcutaneous vosoritide therapy in children with achondroplasia: a randomised, double-blind, phase 3, placebo-controlled, multicentre trial
第一作者:
Savarirayan, Ravi
作者:
Savarirayan, Ravi [1]
;
Tofts, Louise [2]
;
Irving, Melita [3]
;
Wilcox, William [4]
;
Bacino, Carlos A. [5]
;
Hoover-Fong, Julie [6]
;
Ullot Font, Rosendo [7]
;
Harmatz, Paul [8]
;
Rutsch, Frank [9]
;
Bober, Michael B. [10]
;
Polgreen, Lynda E. [11]
;
Ginebreda, Ignacio [12]
;
Mohnike, Klaus [13]
;
Charrow, Joel [14]
;
Hoernschemeyer, Daniel [15]
;
Ozono, Keiichi [16]
;
Alanay, Yasemin [17]
;
Arundel, Paul [18]
;
Kagami, Shoji [19]
;
Yasui, Natsuo [20]
;
White, Klane K. [21]
;
Saal, Howard M. [22]
;
Leiva-Gea, Antonio [23]
;
Luna-Gonzalez, Felipe [24]
;
Mochizuki, Hiroshi [25]
;
Basel, Donald [26]
;
Porco, Dania M. ;
Jayaram, Kala ;
Fisheleva, Elena ;
Huntsman-Labed, Alice ;
Day, Jonathan
作者单位:
Royal Childrens Hosp, Murdoch Childrens Res Inst, Parkville, Vic, Australia
[1]
Childrens Hosp Westmead, Kids Rehab, Westmead, NSW, Australia
[2]
Guys & St Thomas NHS Fdn Trust, Evelina Childrens Hosp, London, England
[3]
Emory Univ, Atlanta, GA 30322 USA
[4]
Baylor Coll Med, Houston, TX 77030 USA
[5]
Johns Hopkins Univ, McKusick Nathans Dept Genet Med, Baltimore, MD USA
[6]
Hosp St Joan de Deu, Barcelona, Spain
[7]
UCSF Benioff Childrens Hosp Oakland, Oakland, CA USA
[8]
Muenster Univ Childrens Hosp, Dept Gen Pediat, Munster, Germany
[9]
Nemours Alfred I du Pont Hosp Children, Wilmington, DE USA
[10]
Harbor UCLA Med Ctr, Lundquist Inst Biomed Innovat, Torrance, CA 90509 USA
[11]
Hosp Univ Quiron Dexeus, Barcelona, Spain
[12]
Otto von Guericke Univ, Magdeburg, Germany
[13]
Univ Missouri, Columbia, MO USA
[14]
Osaka Univ Hosp, Osaka, Japan
[15]
Acibadem Mehmet Ali Aydiniar Univ, Sch Med, Istanbul, Turkey
[16]
Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL 60611 USA
[17]
Sheffield Childrens NHS Fdn Trust, Sheffield Childrens Hosp, Sheffield, S Yorkshire, England
[18]
Tokushima Univ Hosp, Tokushima, Japan
[19]
Seattle Childrens Hosp, Seattle, WA USA
[20]
Univ Cincinnati, Coll Med, Cincinnati Childrens Hosp Med Ctr, Cincinnati, OH USA
[21]
Hosp Univ Virgen de la Victoria, Malaga, Spain
[22]
Saitama Childrens Hosp, Saitama, Japan
[23]
Med Coll Wisconsin, Milwaukee, WI 53226 USA
[24]
BioMarin Pharmaceut, Novato, CA USA
[25]
BioMarin UK, London, England
[26]
发布时间
2022-09-11
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