Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency
第一作者:
Maddalena,Migliavacca
作者:
Maddalena,Migliavacca [1]
;
Federica,Barzaghi [2]
;
Claudia,Fossati [3]
;
Paola M. V.,Rancoita [4]
;
Michela,Gabaldo [5]
;
Francesca,Dionisio [6]
;
Stefania,Giannelli [7]
;
Federica Andrea,Salerio [8]
;
Francesca,Ferrua [9]
;
Francesca,Tucci [10]
;
Valeria,Calbi [11]
;
Vera,Gallo [12]
;
Salvatore,Recupero [13]
;
Giulia,Consiglieri [14]
;
Roberta,Pajno [15]
;
Maria,Sambuco [16]
;
Alessio,Priolo [17]
;
Chiara,Ferri [18]
;
Vittoria,Garella [19]
;
Ilaria,Monti [20]
;
Paolo,Silvani [21]
;
Silvia,Darin [22]
;
Miriam,Casiraghi [23]
;
Ambra,Corti [24]
;
Stefano,Zancan ;
Margherita,Levi ;
Daniela,Cesana ;
Filippo,Carlucci ;
Anna,Pituch-Noworolska ;
Dalia,AbdElaziz ;
Ulrich,Baumann ;
Andrea,Finocchi ;
Caterina,Cancrini ;
Saverio,Ladogana ;
Andrea,Meinhardt ;
Isabelle,Meyts ;
Davide,Montin ;
Lucia Dora,Notarangelo ;
Fulvio,Porta ;
Marlène,Pasquet ;
Carsten,Speckmann ;
Polina,Stepensky ;
Alberto,Tommasini ;
Marco,Rabusin ;
Zeynep,Karakas ;
Miguel,Galicchio ;
Lucia,Leonardi ;
Marzia,Duse ;
Sukru Nail,Guner ;
Clelia,Di Serio ;
Fabio,Ciceri ;
Maria Ester,Bernardo ;
Alessandro,Aiuti ;
Maria Pia,Cicalese
作者单位:
Department of Pediatrics, Faculty of Medicine,Cairo University
[1]
Department of Paediatric Pulmonology, Allergy and Neonatology,Hannover Medical School
[2]
Department of Pediatrics, Hematology/Oncology Unit, Istanbul School of Medicine,Istanbul University
[3]
Allergy and Immnunology Service,Hospital de Ni?os VJ Vilela
[4]
Department of Maternal, Infantile and Urological Sciences,Sapienza University of Rome
[5]
San Raffaele Telethon Institute for Gene Therapy (SR-Tiget),IRCCS San Raffaele Scientific Institute
[6]
University Centre for Statistics in the Biomedical Sciences (CUSSB),Vita-Salute San Raffaele
[7]
Fondazione Telethon
[8]
Division of Pediatric Allergy and Immunology, Faculty of Medicine,Necmettin Erbakan University
[9]
Research Unit of Primary Immunodeficiencies, Academic Department of Pediatrics, Bambino Ges
[10]
Paediatric Onco-haematology Unit, ‘Casa Sollievo della Sofferenza’ Hospital,IRCCS
[11]
Department of Pediatric Hematology and Oncology, Medical Center,University Hospital Giessen
[12]
Laboratory of Inborn Errors of Immunity, Department of Microbiology, Immunology and Transplantation
[13]
Department of Pediatric and Public Health Sciences,University of Torino
[14]
Università Vita-Salute San Raffaele
[15]
Department of Anesthesia and Critical Care,IRCCS San Raffaele Scientific Institute
[16]
Medical Direction,Children’s Hospital, ASST-Spedali Civili
[17]
Pediatric Oncology-Hematology and BMT Unit,Spedali Civili di Brescia
[18]
Pediatric Hematology and Immunology,Children’s Hospital
[19]
Institute for Immunodeficiency, Center for Chronic Immunodeficiency (CCI), Faculty of Medicine
[20]
Department of Bone Marrow Transplantation and Cancer Immunotherapy and Faculty of Medicine,Hadassah
[21]
Department of Pediatrics, Institute for Maternal and Child Health,IRCCS Burlo Garofolo
[22]
Department of Medical Biotechnologies,University of Siena
[23]
Department of Immunology,University Children’s Hospital of Cracow
[24]
发布时间
2024-05-23
- 浏览2
Nature medicine
Nature medicine
488-497页
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