作者:
Wagner, Kathryn R. [1]
;
Abdel-Hamid, Hoda Z. [2]
;
Mah, Jean K. [3]
;
Campbell, Craig [4]
;
Guglieri, Michela [5]
;
Muntoni, Francesco [6]
;
Takeshima, Yasuhiro [7]
;
McDonald, Craig M. [8]
;
Kostera-Pruszczyk, Anna [9]
;
Karachunski, Peter [10]
;
Butterfield, Russell J. [11]
;
Mercuri, Eugenio [12]
;
Fiorillo, Chiara [13]
;
Bertini, Enrico S. [14]
;
Tian, Cuixia [15]
;
Statland, Jeffery [16]
;
Sadosky, Alesia B. [17]
;
Purohit, Vivek S. [18]
;
Sherlock, Sarah P. [19]
;
Palmer, Jeffrey P. ;
Binks, Michael ;
Charnas, Lawrence ;
Marraffino, Shannon ;
Wong, Brenda L.
作者单位:
Pfizer Inc, Cambridge, MA USA
[1]
Univ Cincinnati, Coll Med, Cincinnati Childrens Hosp Med Ctr, Cincinnati, OH USA
[2]
Univ Massachusetts, Sch Med, Worcester, MA USA
[3]
IRCCS Giannina Gaslini, Genoa, Italy
[4]
Univ Kansas, Med Ctr, Kansas City, KS 66103 USA
[5]
UCL, Great Ormond St Inst Child Hlth, NIHR Great Ormond St Hosp Biomed Res Ctr, London, England
[6]
Univ Calgary, Alberta Childrens Hosp, Cumming Sch Med, Calgary, AB, Canada
[7]
Univ Utah, Sch Med, Salt Lake City, UT USA
[8]
Pfizer Inc, New York, NY USA
[9]
Univ Pittsburgh, Pittsburgh, PA USA
[10]
Catholic Univ, Paediat Neurol, Rome, Italy
[11]
Newcastle Univ, John Walton Musc Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, England
[12]
Hyogo Coll Med, Nishinomiya, Hyogo, Japan
[13]
Univ Western Ontario, Dept Pediat Clin Neurol Sci & Epidemiol, Childrens Hosp, London Hlth Sci Ctr
[14]
Med Univ Warsaw, Dept Neurol, Warsaw, Poland
[15]
Univ Minnesota, Minneapolis, MN USA
[16]
IRCCS, Bambino Gesu Childrens Res Hosp, Genoa, Italy
[17]
Ctr Genet Muscle Disorders, Baltimore, MD 21205 USA
[18]
Childrens Hosp, Lawson Hlth Res Inst, London, ON, Canada
[19]
发布时间
2021-01-12