作者:
Zimran,A. [1]
;
Pastores,G.M. [2]
;
Tylki-Szymanska,A. [3]
;
Hughes,D.A. [4]
;
Elstein,D. [5]
;
Mardach,R. [6]
;
Eng,C. [7]
;
Smith,L. [8]
;
Heisel-Kurth,M. [9]
;
Charrow,J. [10]
;
Harmatz,P. [11]
;
Fernhoff,P. [12]
;
Rhead,W. [13]
;
Longo,N. [14]
;
Giraldo,P. [15]
;
Ruiz,J.A. [16]
;
Zahrieh,D. ;
Crombez,E. ;
Grabowski,G.A.
作者单位:
Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER), Hospital Universitario
[1]
Baylor College of Medicine, Houston, TX, United States
[2]
University of Utah, Salt Lake City, UT, United States
[3]
Children's Hospitals of Minnesota, Minneapolis, MN, United States
[4]
Children's Mercy Hospital, Kansas City, MO, United States
[5]
Shire Human Genetic Therapies, Lexington, MA, United States
[6]
Cincinnati Children's Hospital Medical Center, Cincinnati, OH, United States
[7]
New York University School of Medicine, New York, NY, United States
[8]
Royal Free Hospital, University College London School of Medicine, London, United Kingdom
[9]
Kaiser Permanente, Los Angeles, CA, United States
[10]
Children's Hospital Oakland, Oakland, CA, United States
[11]
Children's Hospital of Wisconsin, Milwaukee, WI, United States
[12]
Shaare Zedek Medical Center and Hebrew University-Hadassah Medical School, Jerusalem, Israel
[13]
Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, IL, United States
[14]
Children's Memorial Health Institute, Warsaw, Poland
[15]
Emory University, Decatur, GA, United States
[16]
发布时间
2019-03-16