作者:
Ferla, Rita [1]
;
Claudiani, Pamela [2]
;
Savarese, Marco [3]
;
Kozarsky, Karen [4]
;
Parini, Rossella [5]
;
Scarpa, Maurizio [6]
;
Donati, Maria Alice [7]
;
Sorge, Giovanni [8]
;
Hopwood, John J. [9]
;
Parenti, Giancarlo [10]
;
Fecarotta, Simona ;
Nigro, Vincenzo ;
Sivri, Hatice Serap ;
Van der Ploeg, Ans ;
Andria, Generoso ;
Brunetti-Pierri, Nicola ;
Auricchio, Alberto
作者单位:
AO San Gerardo, Fdn MBBM, Rare Metab Dis Unit, I-20900 Monza, Italy
[1]
Univ Padua, Dept Pediat, I-35128 Padua, Italy
[2]
Univ Florence, Psychol Sect, Dept Neurosci Psychol Drug & Childs Hlth, I-50135 Florence, Italy
[3]
REGENXBIO, Washington, DC 20006 USA
[4]
Hacettepe Univ, Fac Med, Dept Pediat, Sect Metab Disorders, TR-06100 Ankara, Turkey
[5]
Univ Hosp, Erasmus Med Ctr, Ctr Lysosomal & Metab Dis, Dept Pediat, NL-3015 Rotterdam, Netherlands
[6]
Univ Catania, Dept Pediat, I-95123 Catania, Italy
[7]
South Australian Hlth & Med Res Inst, Lysosomal Dis Res Unit, Adelaide, SA 5001, Australia
[8]
Univ Naples Federico II, Dept Translat Med, Sect Pediat, I-80131 Naples, Italy
[9]
Telethon Inst Genet & Med, I-80078 Naples, Italy
[10]
发布时间
2015-06-10