作者:
Maryam,Oskoui [1]
;
John W.,Day [2]
;
Nicolas,Deconinck [3]
;
Elena S.,Mazzone [4]
;
Andres,Nascimento [5]
;
Kayoko,Saito [6]
;
Carole,Vuillerot [7]
;
Giovanni,Baranello [8]
;
Nathalie,Goemans [9]
;
Janbernd,Kirschner [10]
;
Anna,Kostera-Pruszczyk [11]
;
Laurent,Servais [12]
;
Gergely,Papp [13]
;
Ksenija,Gorni [14]
;
Heidemarie,Kletzl [15]
;
Carmen,Martin [16]
;
Tammy,McIver [17]
;
Renata S.,Scalco ;
Hannah,Staunton ;
Wai Yin,Yeung ;
Paulo,Fontoura ;
Eugenio,Mercuri
作者单位:
Roche Products Ltd
[1]
Pharma Development Neurology,F. Hoffmann-La Roche Ltd
[2]
PDMA Neuroscience and Rare Disease,F. Hoffmann-La Roche Ltd
[3]
Pediatric Neurology Institute,Catholic University and Nemo Pediatrico, Fondazione Policlinico
[4]
Roche Pharmaceutical Research and Early Development,Roche Innovation Center Basel
[5]
Departments of Pediatrics and Neurology and Neurosurgery,McGill University
[6]
Department of Neurology,Stanford University
[7]
Neuromuscular Reference Center,UZ Gent
[8]
Neuromuscular Unit, Neuropaediatrics Department,Hospital Sant Joan de Déu, Fundacion Sant Joan de
[9]
Institute of Medical Genetics,Tokyo Women’s Medical University
[10]
Department of Pediatric Physical Medicine and Rehabilitation,H?pital Mère Enfant, CHU-Lyon
[11]
The Dubowitz Neuromuscular Centre, NIHR Great Ormond Street Hospital Biomedical Research Centre
[12]
Neuromuscular Reference Centre, Department of Paediatrics and Child Neurology,University Hospitals
[13]
Department of Neuropediatrics and Muscle Disorders, Faculty of Medicine,Medical Center–University
[14]
Department of Neurology,Medical University of Warsaw
[15]
I-Motion-H?pital Armand Trousseau
[16]
Pharma Development, Safety,F. Hoffmann-La Roche Ltd
[17]
发布时间
2023-09-09