Compacted DNA nanoparticles administered to the nasal mucosa of cystic fibrosis subjects are safe and demonstrate partial to complete cystic fibrosis transmembrane regulator reconstitution.
作者:
主题词
投药, 鼻内(Administration, Intranasal);C反应蛋白质(C-Reactive Protein);临床方案(Clinical Protocols);补体系统蛋白质类(Complement System Proteins);囊性纤维化(Cystic Fibrosis);囊性纤维化跨膜传导调节因子(Cystic Fibrosis Transmembrane Conductance Regulator);DNA(DNA);双盲法(Double-Blind Method);基因转移技术(Gene Transfer Techniques);遗传载体(Genetic Vectors);白细胞介素6(Interleukin-6);纳米结构(Nanostructures);鼻灌洗液(Nasal Lavage Fluid);鼻黏膜(Nasal Mucosa);聚合酶链反应(Polymerase Chain Reaction);时间因素(Time Factors)
DOI
10.1089/hum.2004.15.1255
PMID
15684701
发布时间
2022-03-09
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Human gene therapy
1255-69页
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