Neutralizing antibodies against adeno-associated virus examined prospectively in pediatric patients with hemophilia.
第一作者:
C,Li
第一单位:
Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
作者:
医学主题词
抗体, 中和(Antibodies, Neutralizing);抗体, 病毒(Antibodies, Viral);细胞系(Cell Line);儿童(Child);依赖病毒(Dependovirus);随访研究(Follow-Up Studies);遗传载体(Genetic Vectors);血友病A(Hemophilia A);人类(Humans);男(雄)性(Male);细小病毒科感染(Parvoviridae Infections);血清流行病学研究(Seroepidemiologic Studies)
DOI
10.1038/gt.2011.90
PMID
21697954
发布时间
2022-04-08
基金项目
1R01AI080726/AI/NIAID NIH HHS/United States
5R01AI072176/AI/NIAID NIH HHS/United States
5R01DK084033/DK/NIDDK NIH HHS/United States
5U54AR056953/AR/NIAMS NIH HHS/United States
R00069/PHS HHS/United States
U27/CCU812106/PHS HHS/United States
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Gene therapy
288-94页
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