Long-term restoration of cardiac dystrophin expression in golden retriever muscular dystrophy following rAAV6-mediated exon skipping.-论文-万方医学网

作者： Lawrence T,Bish ^[1] ; Meg M,Sleeper ; Sean C,Forbes ; Bingjing,Wang ; Caryn,Reynolds ; Gretchen E,Singletary ; Dennis,Trafny ; Kevin J,Morine ; Julio,Sanmiguel ; Sylvain,Cecchini ; Tamas,Virag ; Adeline,Vulin ; Cyriaque,Beley ; Janet,Bogan ; James M,Wilson ; Krista,Vandenborne ; Joe N,Kornegay ; Glenn A,Walter ; Robert M,Kotin ; Luis,Garcia ; H Lee,Sweeney

作者单位： Department of Physiology, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, USA. bish@mail.med.upenn.edu ^[1]

主题词选择性剪接(Alternative Splicing);动物(Animals);细胞系(Cell Line);依赖病毒(Dependovirus);疾病模型, 动物(Disease Models, Animal);狗(Dogs);肌营养不良蛋白(Dystrophin);超声心动描记术(Echocardiography);外显子(Exons);纤维化(Fibrosis);基因表达(Gene Expression);基因顺序(Gene Order);基因转移技术(Gene Transfer Techniques);遗传载体(Genetic Vectors);基因组, 病毒(Genome, Viral);人类(Humans);磁共振成像(Magnetic Resonance Imaging);肌营养不良, 杜氏(Muscular Dystrophy, Duchenne);心肌(Myocardium);RNA, 信使(RNA, Messenger)

DOI 10.1038/mt.2011.264

PMID 22146342

发布时间 2024-05-08

检索历史清除

Long-term restoration of cardiac dystrophin expression in golden retriever muscular dystrophy following rAAV6-mediated exon skipping.

Molecular therapy

相似文献

Molecular therapy

相关期刊

参考文献：
指定格式：	NoteExpress EndNote RefWorks NoteFirst

检索历史 清除

Long-term restoration of cardiac dystrophin expression in golden retriever muscular dystrophy following rAAV6-mediated exon skipping.

Molecular therapy

相似文献

Molecular therapy

相关期刊

检索历史清除