Retroviral-vector-mediated gene therapy to mucopolysaccharidosis I mice improves sensorimotor impairments and other behavioral deficits.
第一作者:
Guilherme,Baldo
第一单位:
Department of Internal Medicine, Washington University School of Medicine, St. Louis, MO 63110, USA.
作者:
医学主题词
动物(Animals);动物, 新生(Animals, Newborn);行为, 动物(Behavior, Animal);脑(Brain);基因转移技术(Gene Transfer Techniques);遗传载体(Genetic Vectors);艾杜糖醛酸酶(Iduronidase);精神障碍(Mental Disorders);小鼠(Mice);小鼠, 近交C57BL(Mice, Inbred C57BL);运动神经元病(Motor Neuron Disease);运动神经元(Motor Neurons);黏多糖累积病Ⅰ型(Mucopolysaccharidosis I);逆转录病毒科(Retroviridae)
DOI
10.1007/s10545-012-9530-x
PMID
22983812
发布时间
2022-03-09
基金项目
P30 NS057105/NS/NINDS NIH HHS/United States
P30 DC004665/DC/NIDCD NIH HHS/United States
R56 DK066448/DK/NIDDK NIH HHS/United States
R01 DK066448/DK/NIDDK NIH HHS/United States
DK66448/DK/NIDDK NIH HHS/United States
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