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TALENs Facilitate Single-step Seamless SDF Correction of F508del CFTR in Airway Epithelial Submucosal Gland Cell-derived CF-iPSCs.

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第一作者: Shingo,Suzuki
第一单位: Department of Otolaryngology - Head and Neck Surgery, University of California-San Francisco, San Francisco, California, USA.;Department of Molecular Medicine, Graduate School of Pharmaceutical Sciences, Kumamoto University, Kumamoto, Japan.
作者单位: Department of Otolaryngology - Head and Neck Surgery, University of California-San Francisco, San Francisco, California, USA.;Department of Molecular Medicine, Graduate School of Pharmaceutical Sciences, Kumamoto University, Kumamoto, Japan. [1] Department of Otolaryngology - Head and Neck Surgery, University of California-San Francisco, San Francisco, California, USA.;California Pacific Medical Center Research Institute, San Francisco, California, USA. [2] Childrens Hospital Oakland Research Institute, Oakland, California, USA. [3] Department of Otolaryngology - Head and Neck Surgery, University of California-San Francisco, San Francisco, California, USA. [4] Department of Otolaryngology - Head and Neck Surgery, University of California-San Francisco, San Francisco, California, USA.;Present address: Graduate Program in Biochemistry, Molecular, Cellular, and Developmental Biology, University of California-Davis, Davis, California, USA. [5] California Pacific Medical Center Research Institute, San Francisco, California, USA.;Present address: Molecular Department, Hunter Laboratories, Campbell, California, USA. [6] Liver Center, University of California-San Francisco, San Francisco, California, USA.;Present address: Heinrich-Heine-Universität Düsseldorf, Institut für Genetik, Düsseldorf, Germany. [7] Department of Otolaryngology - Head and Neck Surgery, University of California-San Francisco, San Francisco, California, USA.;California Pacific Medical Center Research Institute, San Francisco, California, USA.;Present address: Graduate Program in the Department of Biosystems Science and Engineering, ETH, Zürich, Switzerland. [8] Department of Laboratory Medicine, University of California-San Francisco, San Francisco, California, USA. [9] Department of Laboratory Medicine, University of California-San Francisco, San Francisco, California, USA.;Liver Center, University of California-San Francisco, San Francisco, California, USA.;Blood Systems Research Institute, San Francisco, California, USA. [10] Blood Systems Research Institute, San Francisco, California, USA. [11] Department of Medicine, University of California-San Francisco, San Francisco, California, USA. [12] Department of Biomedical Engineering, Georgia Institute of Technology, Atlanta, Georgia, USA. [13] Department of Pediatrics, Stanford University, Stanford, California, USA. [14] Department of Molecular Medicine, Graduate School of Pharmaceutical Sciences, Kumamoto University, Kumamoto, Japan. [15] Department of Medicine, University of California-San Francisco, San Francisco, California, USA.;Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, Helen Diller Family Comprehensive Cancer Center, Institute for Human Genetics, Cardiovascular Research Institute, University of California-San Francisco, San Francisco, California, USA. [16] Department of Otolaryngology - Head and Neck Surgery, University of California-San Francisco, San Francisco, California, USA.;California Pacific Medical Center Research Institute, San Francisco, California, USA.;Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, Helen Diller Family Comprehensive Cancer Center, Institute for Human Genetics, Cardiovascular Research Institute, University of California-San Francisco, San Francisco, California, USA.;Department of Pediatrics, University of Vermont College of Medicine, Burlington, Vermont, USA. [17]
DOI 10.1038/mtna.2015.43
PMID 26730810
发布时间 2024-09-22
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