作者:
Yafeng,Song [1]
;
Leon,Morales [1]
;
Alock S,Malik [1]
;
Andrew F,Mead [1]
;
Christopher D,Greer [1]
;
Marilyn A,Mitchell [1]
;
Mihail T,Petrov [1]
;
Leonard T,Su [1]
;
Margaret E,Choi [1]
;
Shira T,Rosenblum [1]
;
Xiangping,Lu [1]
;
Daniel J,VanBelzen [1]
;
Ranjith K,Krishnankutty [1]
;
Frederick J,Balzer [1]
;
Emanuele,Loro [2]
;
Robert,French [1]
;
Kathleen J,Propert [3]
;
Shangzhen,Zhou [4]
;
Benjamin W,Kozyak [1]
;
Peter P,Nghiem [5]
;
Tejvir S,Khurana [6]
;
Joe N,Kornegay [2]
;
Hansell H,Stedman [6]
作者单位:
Department of Surgery, Pennsylvania Muscle Institute, Penn Cardiovascular Institute, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA.
[1]
Department of Physiology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA.
[2]
Department of Biostatistics, Epidemiology and Informatics, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA.
[3]
Department of Ophthalmology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA.
[4]
Department of Anesthesiology and Critical Care Medicine, The Children's Hospital of Philadelphia, Philadelphia, PA, USA.
[5]
Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Texas A&M Institute for Neuroscience, Texas A&M University, College Station, TX, USA.
[6]
Department of Surgery, Pennsylvania Muscle Institute, Penn Cardiovascular Institute, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. hstedman@pennmedicine.upenn.edu.
[7]
Corporal Michael J. Crescenz Veterans Affairs Medical Center, Philadelphia, PA, USA. hstedman@pennmedicine.upenn.edu.
[8]
主题词
动物(Animals);依赖病毒(Dependovirus);疾病模型, 动物(Disease Models, Animal);狗(Dogs);肌营养不良蛋白(Dystrophin);人类(Humans);小鼠(Mice);小鼠, 近交mdx(Mice, Inbred mdx);肌收缩(Muscle Contraction);肌, 骨骼(Muscle, Skeletal);肌营养不良(Muscular Dystrophies);肌营养不良, 动物(Muscular Dystrophy, Animal);肌营养不良, 杜氏(Muscular Dystrophy, Duchenne);转基因(Transgenes);肌营养不良蛋白相关蛋白质(Utrophin)
DOI
10.1038/s41591-019-0594-0
PMID
31591596
发布时间
2021-05-25