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Treatment with Nusinersen - Challenges Regarding the Indication for Children with SMA Type 1.

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第一作者: Astrid,Pechmann
第一单位: Department of Neuropediatrics and Muscle Disorders, Medical Center - University of Freiburg, Faculty of Medicine, University of Freiburg, Germany.
作者单位: Department of Neuropediatrics and Muscle Disorders, Medical Center - University of Freiburg, Faculty of Medicine, University of Freiburg, Germany. [1] Department of Pediatrics I, Division of Pediatric Neurology, Medical University of Innsbruck, Innsbruck, Austria. [2] Department of Pediatrics, Neuropediatrics, Kaiser Franz Josef Krankenhaus mit Gottfried von Preyer Children Hospital, Vienna, Austria. [3] Department of Pediatric Neurology, Saarland University Medical Center, Homburg, Germany. [4] Department of Pediatrics and Adolescent Medicine, Division of General Pediatrics, Medical University of Graz, Graz, Austria. [5] Abteilung Neuropädiatrie, Medizinische Fakultät Carl Gustav Carus, Technische Universität Dresden, Germany. [6] Children's Hospital of Eastern Switzerland, St Gallen, Switzerland. [7] Department of Pediatrics and Adolescent Medicine, Division of Pediatric Neurology, University Medical Center Göttingen, Georg August University, Robert Koch Strasse 40, Göttingen, 37075, Germany. [8] Department of Paediatric Neurology, University Children's Hospital, Tübingen, Germany. [9] Department of Pediatrics, Neuropediatrics, University Medical Center Hamburg-Eppendorf, Hamburg, Germany. [10] Department of Neuropaediatrics, University Children's Hospital, Ruhr-University Bochum, Bochum, Germany. [11] Department of Pediatrics and Neuropediatrics, DRK Klinikum Westend, Berlin, Germany. [12] Department of Neuropediatrics, Dr. v. Haunersche Kinderklinik, University Children's Hospital, LMU, München, Germany. [13] Department for Pediatric Neurology, Center for Child and Adolescent Medicine Olgahospital, Psychosomatic and Pain Medicine, Child Pain Center Baden-Württemberg, Klinikum Stuttgart, Stuttgart, Germany. [14] Department of Pediatrics, State Hospital of Bregenz (LKH Bregenz), Bregenz, Austria. [15] Department of Neuropediatrics, Klinikum Kassel, Kassel, Germany. [16] Department of Neuropediatrics, University Children's Hospital Muenster, Muenster, Germany. [17] Department of Pediatrics, Klinikum Wels-Grieskirchen, Wels, Austria. [18] Department of Neuropediatrics, Charité - Universitätsmedizin Berlin, Berlin, Germany. [19] Department of Neuropediatrics, Kliniken der Stadt Köln, Children's Hospital, Cologne, Germany. [20] Neuropediatrics Section of the Department of Pediatrics, Asklepios Clinic Hamburg, Nord-Heidberg, Hamburg, Germany. [21] Department of Pediatrics, Ulm University, Ulm, Germany. [22] Kinderzentrum St. Martin - Social Paediatric Centre Regensburg, Regensburg, Germany. [23] Department of Neuropediatrics, Children's Hospital 1, University of Duisburg-Essen, Essen, Germany. [24] Department of Neuropediatrics, University Hospital Bonn, Bonn, Germany. [25]
DOI 10.3233/JND-190441
PMID 31744015
发布时间 2020-10-13
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Journal of neuromuscular diseases

Journal of neuromuscular diseases

2020年7卷1期

41-46页

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