第一作者:
Hasan,Hashem
第一单位:
Department of Pediatrics, Division of Pediatric Hematology and Oncology, Bone Marrow Transplant Unit, King Hussein Cancer Center (KHCC), P.O Box 1269, Amman, 11941, Jordan. hh.08847@khcc.jo.
作者:
Hasan,Hashem [1]
;
Giorgia,Bucciol [2]
;
Seza,Ozen [3]
;
Sule,Unal [4]
;
Ikbal Ok,Bozkaya [5]
;
Nurten,Akarsu [6]
;
Mervi,Taskinen [7]
;
Minna,Koskenvuo [8]
;
Janna,Saarela [9]
;
Dimana,Dimitrova [10]
;
Dennis D,Hickstein [11]
;
Amy P,Hsu [12]
;
Steven M,Holland [12]
;
Robert,Krance [13]
;
Ghadir,Sasa [13]
;
Ashish R,Kumar [14]
;
Ingo,Müller [15]
;
Monica Abreu,de Sousa [15]
;
Selket,Delafontaine [2]
;
Leen,Moens [16]
;
Florian,Babor [17]
;
Federica,Barzaghi [18]
;
Maria Pia,Cicalese [19]
;
Robbert,Bredius [20]
;
Joris,van Montfrans [21]
;
Valentina,Baretta [22]
;
Simone,Cesaro [22]
;
Polina,Stepensky [23]
;
Neven,Benedicte [24]
;
Despina,Moshous [24]
;
Guillaume,Le Guenno [25]
;
David,Boutboul [26]
;
Jignesh,Dalal [27]
;
Joel P,Brooks [28]
;
Elif,Dokmeci [29]
;
Jasmeen,Dara [30]
;
Carrie L,Lucas [28]
;
Sophie,Hambleton [31]
;
Keith,Wilson [32]
;
Stephen,Jolles [33]
;
Yener,Koc [34]
;
Tayfun,Güngör [35]
;
Caroline,Schnider [36]
;
Fabio,Candotti [37]
;
Sandra,Steinmann [38]
;
Ansgar,Schulz [38]
;
Chip,Chambers [39]
;
Michael,Hershfield [40]
;
Amanda,Ombrello [41]
;
Jennifer A,Kanakry [10]
;
Isabelle,Meyts [42]
作者单位:
Department of Pediatrics, Division of Pediatric Hematology and Oncology, Bone Marrow Transplant Unit, King Hussein Cancer Center (KHCC), P.O Box 1269, Amman, 11941, Jordan. hh.08847@khcc.jo.
[1]
Department of Pediatrics, ERN RITA Core Center, University Hospitals Leuven, Herestraat 49, 3000, Leuven, Belgium.;Department of Microbiology, Immunology and Transplantation, Laboratory for Inborn Errors of Immunity, University Hospitals Leuven, Herestraat 49, 3000, Leuven, Belgium.
[2]
Department of Pediatric Rheumatology, Hacettepe University, Ankara, Turkey.;Hacettepe University Vasculitis Research Center, Ankara, Turkey.
[3]
Department of Pediatric Hematology, Research Center for Fanconi Anemia and Other Inherited Bone Marrow Failure Syndromes, Hacettepe University, Ankara, Turkey.
[4]
Division of Pediatric Hematology and Oncology, Bone Marrow Transplant Unit, University of Health Sciences, Ankara City Hospital, Ankara, Turkey.
[5]
Department of Medical Genetics, Hacettepe University, Sihhiye, 06100, Ankara, Turkey.
[6]
Division of Pediatric Hematology, Oncology and Stem Cell Transplantation, Helsinki University Hospital, Helsinki, Finland.
[7]
Pediatric Hematology, Oncology and Stem Cell Transplantation, Children and Adolescents, Helsinki University Hospital, Helsinki, Finland.
[8]
Institute for Molecular Medicine Finland, HiLIFE, University of Helsinki, Helsinki, Finland.;Centre for Molecular Medicine Norway, University of Oslo, Oslo, Norway.
[9]
Experimental Transplantation and Immunotherapy Branch, National Cancer Institute of the National Institutes of Health, Bethesda, MD, USA.
[10]
Immune Deficiency Cellular Therapy Program, CCR, NCI, MD, Bethesda, USA.
[11]
Laboratory of Clinical Infectious Diseases, National Institute of Allergy and Infectious Diseases, Bethesda, MD, USA.
[12]
Cell and Gene Therapy, Baylor College of Medicine, Houston, TX, USA.
[13]
Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.;University of Cincinnati College of Medicine, Cincinnati, OH, USA.
[14]
Division of Pediatric Stem Cell Transplantation and Immunology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
[15]
Department of Microbiology, Immunology and Transplantation, Laboratory for Inborn Errors of Immunity, University Hospitals Leuven, Herestraat 49, 3000, Leuven, Belgium.
[16]
Department of Pediatric Oncology, Hematology and Clinical Immunology, Center for Child and Adolescent Health, Medical Faculty, Heinrich-Heine-University, Düsseldorf, Germany.
[17]
San Raffaele Telethon Institute for Gene Therapy (TIGET), Pediatric Immunohematology and Bone Marrow Transplantation Unit, IRCCS San Raffaele Scientific Institute Milan, Milan, Italy.
[18]
Pediatric Immunohematology and Bone Marrow Transplantation Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
[19]
Department of Pediatrics, Willem-Alexander Children's Hospital, Leiden University Medical Center, Leiden, Netherlands.
[20]
Department of Pediatric Immunology and Infectious Diseases, Wilhelmina Children's Hospital, University Medical Centre Utrecht, Utrecht, Netherlands.
[21]
Pediatric Hematology Oncology, Department of Mother and Child, Azienda Ospedaliera Universitaria Integrata, Verona, Italy.
[22]
Department of Bone Marrow Transplantation and Cancer Immunotherapy, Hadassah University Medical Center, Jerusalem, Israel.
[23]
Pediatric Immunology, Hematology and Rheumatology Unit, Hôpital Necker-Enfants Malades, APHP, Paris, France.
[24]
Department of Internal Medicine, University Hospital Estaing, CHU Clermont-Ferrand, Clermont-Ferrand, France.
[25]
Clinical Immunology Department, Hospital Saint Louis, Université de Paris, Paris, France.
[26]
Rainbow Babies and Children's Hospital, Case Western Reserve University, Cleveland, OH, USA.
[27]
Department of Immunobiology, Yale University School of Medicine, New Haven, CT, USA.
[28]
Department of Pediatrics, University of New Mexico, Albuquerque, NM, USA.
[29]
Department of Pediatrics, Division of Allergy, Immunology, Blood and Marrow Transplantation, University of California San Francisco, San Francisco, CA, USA.
[30]
Newcastle University Translational and Clinical Research Institute and Great North Children's Hospital, Newcastle Upon Tyne Hospitals NHS Foundation Trust, , Newcastle Upon Tyne, UK.
[31]
Department of Hematology, University Hospital of Wales, Cardiff, UK.
[32]
Immunodeficiency Centre for Wales, University Hospital of Wales, Cardiff, UK.
[33]
Stem Cell Transplant Unit, Medicana International, Istanbul, Turkey.
[34]
Division of Hematology/Oncology/Immunology, Gene Therapy, and Stem Cell Transplantation, University Children's Hospital Zurich - Eleonore Foundation & Children's Research Center (CRC), Steinwiesstrasse 75, CH-8032, Zurich, Switzerland.
[35]
Pediatric Immuno-Rheumatology of Western Switzerland, Department Women-Mother-Child, Lausanne University Hospital, Lausanne, Switzerland.
[36]
Division of Immunology and Allergy, Lausanne University Hospital and University of Lausanne, Lausanne, Switzerland.
[37]
Department of Pediatrics, University Medical Center Ulm, Ulm, Germany.
[38]
Vanderbilt University Medical Center, Nashville, TN, USA.
[39]
Department of Medicine and Biochemistry, Duke University Medical Center, Durham, NC, USA.
[40]
Metabolic, Cardiovascular, and Inflammatory Disease Genomics Branch, National Human Genome Research Institute (NHGRI), Bethesda, MD, USA.
[41]
Department of Pediatrics, ERN RITA Core Center, University Hospitals Leuven, Herestraat 49, 3000, Leuven, Belgium. isabelle.meyts@uzleuven.be.;Department of Microbiology, Immunology and Transplantation, Laboratory for Inborn Errors of Immunity, University Hospitals Leuven, Herestraat 49, 3000, Leuven, Belgium. isabelle.meyts@uzleuven.be.
[42]
医学主题词
腺苷脱氨酶(Adenosine Deaminase);青少年(Adolescent);成年人(Adult);丙种球蛋白缺乏血症(Agammaglobulinemia);儿童(Child);儿童, 学龄前(Child, Preschool);女(雌)性(Female);移植物抗宿主病(Graft vs Host Disease);造血干细胞移植(Hematopoietic Stem Cell Transplantation);人类(Humans);胞间信号肽类和蛋白质类(Intercellular Signaling Peptides and Proteins);Kaplan-Meiers评估(Kaplan-Meier Estimate);男(雄)性(Male);回顾性研究(Retrospective Studies);重症联合免疫缺陷(Severe Combined Immunodeficiency);治疗结果(Treatment Outcome);青年人(Young Adult)
DOI
10.1007/s10875-021-01098-0
PMID
34324127
发布时间
2025-05-30
- 浏览4
Journal of clinical immunology
Journal of clinical immunology
1633-1647页
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