The Pediatric Precision Oncology INFORM Registry: Clinical Outcome and Benefit for Patients with Very High-Evidence Targets.
作者:
Cornelis M,van Tilburg [1]
;
Elke,Pfaff [2]
;
Kristian W,Pajtler [3]
;
Karin P S,Langenberg [4]
;
Petra,Fiesel [5]
;
Barbara C,Jones [6]
;
Gnana Prakash,Balasubramanian [3]
;
Sebastian,Stark [4]
;
Pascal D,Johann [5]
;
Mirjam,Blattner-Johnson [7]
;
Kathrin,Schramm [6]
;
Nicola,Dikow [3]
;
Steffen,Hirsch [4]
;
Christian,Sutter [5]
;
Kerstin,Grund [8]
;
Arend,von Stackelberg [9]
;
Andreas E,Kulozik [4]
;
Andrej,Lissat [5]
;
Arndt,Borkhardt [10]
;
Roland,Meisel [11]
;
Dirk,Reinhardt [6]
;
Jan-Henning,Klusmann [3]
;
Gudrun,Fleischhack [4]
;
Stephan,Tippelt [5]
;
Dietrich,von Schweinitz [7]
;
Irene,Schmid [6]
;
Christof M,Kramm [4]
;
André O,von Bueren [5]
;
Gabriele,Calaminus [8]
;
Peter,Vorwerk [6]
;
Norbert,Graf [3]
;
Frank,Westermann [4]
;
Matthias,Fischer [5]
;
Angelika,Eggert [7]
;
Birgit,Burkhardt [6]
;
Wilhelm,Wößmann [3]
;
Michaela,Nathrath [4]
;
Stefanie,Hecker-Nolting [5]
;
Michael C,Frühwald [8]
;
Dominik T,Schneider [12]
;
Ines B,Brecht [6]
;
Petra,Ketteler [4]
;
Simone,Fulda [5]
;
Ewa,Koscielniak [7]
;
Michael T,Meister [6]
;
Monika,Scheer [4]
;
Simone,Hettmer [5]
;
Matthias,Schwab [7]
;
Roman,Tremmel [13]
;
Ingrid,Øra [6]
;
Caroline,Hutter [13]
;
Nicolas U,Gerber [13]
;
Olli,Lohi [13]
;
Bernarda,Kazanowska [4]
;
Antonis,Kattamis [5]
;
Maria,Filippidou [14]
;
Bianca,Goemans [6]
;
C Michel,Zwaan [3]
;
Till,Milde [4]
;
Natalie,Jäger [5]
;
Stephan,Wolf [15]
;
David,Reuss [4]
;
Felix,Sahm [5]
;
Andreas,von Deimling [14]
;
Uta,Dirksen [4]
;
Angelika,Freitag [16]
;
Ruth,Witt [4]
;
Peter,Lichter [17]
;
Annette,Kopp-Schneider [4]
;
David T W,Jones [5]
;
Jan J,Molenaar [18]
;
David,Capper [19]
;
Stefan M,Pfister [4]
;
Olaf,Witt [5]
作者单位:
Hopp Children's Cancer Center Heidelberg (KiTZ), Heidelberg, Germany. cornelis.vantilburg@kitz-heidelberg.de.
[1]
Clinical Cooperation Unit Pediatric Oncology, German Cancer Research Center (DKFZ), Heidelberg, Germany.
[2]
Department of Pediatric Oncology, Hematology, Immunology and Pulmonology, Heidelberg University Hospital, Heidelberg, Germany.
[3]
German Cancer Consortium (DKTK), Heidelberg, Germany.
[4]
National Center for Tumor Diseases (NCT) Network, Germany.
[5]
Hopp Children's Cancer Center Heidelberg (KiTZ), Heidelberg, Germany.
[6]
Pediatric Glioma Research Group, German Cancer Research Center (DKFZ), Heidelberg, Germany.
[7]
Division of Pediatric Neurooncology, German Cancer Research Center (DKFZ), Heidelberg, Germany.
[8]
Princess Máxima Center for Pediatric Oncology, Utrecht, the Netherlands.
[9]
Clinical Cooperation Unit Neuropathology, German Cancer Research Center (DKFZ), Heidelberg, Germany.
[10]
Department of Neuropathology, Institute of Pathology, Heidelberg University Hospital, Heidelberg, Germany.
[11]
Swabian Children's Cancer Center, Paediatric and Adolescent Medicine, University Medical Center Augsburg, Augsburg, Germany.
[12]
Institute of Human Genetics, Heidelberg University Hospital, Heidelberg, Germany.
[13]
Pediatric Oncology and Hematology Department, Charité-Campus Virchow Klinikum, Berlin, Germany.
[14]
Clinical Cooperation Unit Pediatric Leukemia, German Cancer Research Center (DKFZ), Heidelberg, Germany.
[15]
Department of Pediatric Oncology and Hematology, Medical Faculty, Heinrich Heine University, Düsseldorf, Germany.
[16]
Division of Pediatric Stem Cell Therapy, Department of Pediatric Oncology, Hematology and Clinical Immunology, Medical Faculty, Heinrich Heine University, Düsseldorf, Germany.
[17]
West German Cancer Center, Pediatrics III, University Hospital Essen, Essen, Germany.
[18]
Department of Pediatric Hematology, Oncology and Hemostaseology, Clinic for Pediatrics, University Hospital of Frankfurt, Goethe-University Frankfurt, Frankfurt/Main, Germany.
[19]
Department of Pediatric Surgery, Dr. von Hauner Children's Hospital, Ludwig-Maximilians-University Munich, Munich, Germany.
[20]
Department of Pediatric Oncology and Hematology, Dr. von Hauner Children's Hospital, Ludwig-Maximilians-University Munich, Munich, Germany.
[21]
Division of Pediatric Hematology and Oncology, University Medical Center Göttingen, Göttingen, Germany.
[22]
Department of Pediatrics, Obstetrics and Gynecology, Division of Pediatric Hematology and Oncology, University Hospital Geneva, Geneva, Switzerland.
[23]
Department of Pediatric Oncology and Hematology, University Hospital Bonn, Bonn, Germany.
[24]
Department of Pediatric Oncology and Hematology, University Hospital Magdeburg, Magdeburg, Germany.
[25]
Department of Pediatric Oncology and Hematology, University Hospital Saarland, Saarland, Germany.
[26]
Division of Neuroblastoma Genomics, German Cancer Research Center (DKFZ), Heidelberg, Germany.
[27]
Department of Experimental Pediatric Oncology, University Hospital Köln, and Center for Molecular Medicine (CMMC), Medical Faculty, Cologne, Germany.
[28]
Clinic of Pediatric Oncology and Hematology, University Hospital Münster, Muenster, Germany.
[29]
Department of Pediatric Oncology and Hematology, University Hospital Hamburg, Hamburg, Germany.
[30]
Department of Pediatric Hematology and Oncology, Klinikum Kassel, Kassel, Germany.
[31]
Department of Pediatrics, Technical University Munich, Munich, Germany.
[32]
Department of Pediatric Oncology, Hematology and Immunology, Klinikum Stuttgart, Olgahospital, Stuttgart, Germany.
[33]
Clinic of Pediatrics, Municipal Hospital Dortmund, Dortmund, Germany.
[34]
Department of Pediatric Oncology and Hematology, University Hospital Tübingen, Tübingen, Germany.
[35]
Institute for Experimental Cancer Research in Pediatrics, Goethe University Frankfurt, Frankfurt, Germany.
[36]
Department of Pediatrics and Adolescent Medicine, Division of Pediatric Hematology and Oncology, University Medical Center Freiburg, Faculty of Medicine, University of Freiburg, Freiburg, Germany.
[37]
Dr. Margarete Fischer-Bosch Institute of Clinical Pharmacology, Stuttgart, Germany.
[38]
Departments of Clinical Pharmacology, Pharmacy and Biochemistry, and Cluster of Excellence iFIT (EXC 2180) "Image-Guided and Functionally Instructed Tumor Therapies," University of Tübingen, Tübingen, Germany.
[39]
Department of Pediatric Oncology and Hematology, Skane University Hospital Lund, and HOPE-ITCC Unit, Pediatric Oncology, Karolinska University Hospital, Stockholm, Sweden.
[40]
St. Anna Children's Hospital, Department of Pediatrics, Medical University of Vienna, and St. Anna Children's Cancer Research Institute (CCRI), Vienna, Austria.
[41]
Department of Oncology, University Children's Hospital, Zurich, Switzerland.
[42]
Tampere Center for Child Health Research and Tays Cancer Centre, Faculty of Medicine and Health Technology, Tampere University, Tampere, Finland.
[43]
Department of Pediatric Hematology/Oncology and BMT, Wroclaw Medical University, Wroclaw, Poland.
[44]
Division of Pediatric Hematology-Oncology, First Department of Pediatrics, National and Kapodistrian University of Athens, Athens, Greece.
[45]
Erasmus MC-Sophia Children's Hospital, Rotterdam, the Netherlands.
[46]
Genomics and Proteomics Core Facility, German Cancer Research Center (DKFZ), Heidelberg, Germany.
[47]
NCT Trial Center, National Center for Tumor Diseases, Heidelberg, Germany, and German Cancer Research Center (DKFZ), Heidelberg, Germany.
[48]
Division of Molecular Genetics, German Cancer Research Center (DKFZ), Heidelberg, Germany.
[49]
Department Biostatistics, German Cancer Research Center (DKFZ), Heidelberg, Germany.
[50]
Utrecht University, Department of Pharmaceutical Sciences, Utrecht, the Netherlands.
[51]
Charité-Universitätsmedizin Berlin, corporate member of Freie Universität Berlin, Humboldt-Universität zu Berlin, and Berlin Institute of Health, Department of Neuropathology, Berlin, Germany.
[52]
DOI
10.1158/2159-8290.CD-21-0094
PMID
34373263
发布时间
2023-01-25
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Cancer discovery
Cancer discovery
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