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Assessing the Relationship of Patient Reported Outcome Measures With Functional Status in Dysferlinopathy: A Rasch Analysis Approach.

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第一作者: Anna G,Mayhew
第一单位: The John Walton Muscular Dystrophy Research Centre, Translational and Clinical Research Institute, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle upon Tyne, United Kingdom.
作者单位: The John Walton Muscular Dystrophy Research Centre, Translational and Clinical Research Institute, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle upon Tyne, United Kingdom. [1] Center for Translational Science, Division of Biostatistics and Study Methodology, Children's National Health System, Washington, DC, United States.;Pediatrics, Epidemiology and Biostatistics, George Washington University, Washington, DC, United States. [2] Center for Translational Science, Division of Biostatistics and Study Methodology, Children's National Health System, Washington, DC, United States. [3] The Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, OH, United States. [4] The Jain Foundation, Seattle, WA, United States. [5] The Children's Hospital at Westmead, The University of Sydney, Sydney, NSW, Australia. [6] Cooperative International Neuromuscular Research Group (CINRG), Children's National Health System, Washington, DC, United States.;Lucile Salter Packard Children's Hospital at Stanford, Neurology, Palo Alto, CA, United States. [7] Department of Neuroscience, University of Padova, Padua, Italy. [8] Physical Medicine and Rehabilitation, Hospital de la Santa Creu i Sant Pau, Barcelona, Spain. [9] Neuroscience Institute, Carolinas Neuromuscular/ALS-MDA Center, Carolinas HealthCare System, Charlotte, NC, United States. [10] Department of Physical Rehabilitation, National Center Hospital, National Center of Neurology and Psychiatry Tokyo, Tokyo, Japan. [11] Institut de Myologie, AP-HP, GH Pitié-Salpêtrière, Paris, France. [12] Neurorehabilitation Unit, Rehabilitation Hospital Universitario Virgen del Rocío Sevilla, Seville, Spain. [13] Department of Neurology, Friedrich-Baur-Institute, Ludwig-Maximilians-University of Munich, Munich, Germany. [14] Department of Neurology, Washington University School of Medicine, St. Louis, MO, United States. [15] Service des Maladies Neuromusculaire et de la SLA, Hôpital de La Timone, Marseille, France. [16] Cooperative International Neuromuscular Research Group (CINRG), Children's National Health System, Washington, DC, United States. [17] ELAN-PHYSIO, Praxis für Physiotherapie Maron, Berlin, Germany. [18] Magnetic Resonance Centre, Institute for Cellular Medicine, Newcastle University, Newcastle upon Tyne, United Kingdom. [19] AIM & CEA NMR Laboratory, Institute of Myology, Pitié-Salpêtrière University Hospital, Paris, France. [20] Charite Muscle Research Unit, Experimental and Clinical Research Center, A Joint Cooperation of the Charité Medical Faculty and the Max Delbrück Center for Molecular Medicine, Berlin, Germany. [21] Department of Neurology and Neurological Sciences, Stanford University School of Medicine, Stanford, CA, United States. [22] Department of Neurology Children's National Health System, Washington, DC, United States.;National Institutes of Health (NINDS), Bethesda, MD, United States. [23] Neuromuscular Unit, Department of Neurology, Hospital U. Virgen del Rocío/Instituto de Biomedicina de Sevilla, Sevilla, Spain. [24] Department of Neurology, National Center Hospital, National Center of Neurology and Psychiatry Tokyo, Tokyo, Japan. [25] Centro de Investigación Biomédica en Red en Enfermedades Raras (CIBERER), Barcelona, Spain.;Neuromuscular Disorders Unit, Neurology Department, Hospital de la Santa Creu i Sant Pau, Barcelona, Spain. [26]
DOI 10.3389/fneur.2022.828525
PMID 35359643
发布时间 2022-04-02
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