换一批Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial.
第一作者：
Michela,Guglieri
第一单位：
John Walton Muscular Dystrophy Research Centre, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle upon Tyne, England.
作者：
Michela,Guglieri [1]
;
Kate,Bushby [1]
;
Michael P,McDermott [2]
;
Kimberly A,Hart [3]
;
Rabi,Tawil [3]
;
William B,Martens [3]
;
Barbara E,Herr [3]
;
Elaine,McColl [4]
;
Chris,Speed [5]
;
Jennifer,Wilkinson [4]
;
Janbernd,Kirschner [6]
;
Wendy M,King [7]
;
Michelle,Eagle [1]
;
Mary W,Brown [3]
;
Tracey,Willis [8]
;
Robert C,Griggs [3]
;
FOR-DMD Investigators of the Muscle Study Group [1]
;
Volker,Straub [1]
;
Henriette,van Ruiten [9]
;
Anne-Marie,Childs [3]
;
Emma,Ciafaloni [10]
;
Perry B,Shieh [11]
;
Stefan,Spinty [12]
;
Lorenzo,Maggi [13]
;
Giovanni,Baranello [14]
;
Russell J,Butterfield [15]
;
I A,Horrocks [16]
;
Helen,Roper [16]
;
Zoya,Alhaswani [17]
;
Kevin M,Flanigan [18]
;
Nancy L,Kuntz [19]
;
Adnan,Manzur [20]
;
Basil T,Darras [21]
;
Peter B,Kang [22]
;
Leslie,Morrison [22]
;
Monika,Krzesniak-Swinarska [23]
;
Jean K,Mah [24]
;
Tiziana E,Mongini [24]
;
Federica,Ricci [25]
;
Maja,von der Hagen [26]
;
Richard S,Finkel [27]
;
Kathleen,O'Reardon [28]
;
Matthew,Wicklund [29]
;
Ashutosh,Kumar [30]
;
Craig M,McDonald [30]
;
Jay J,Han [30]
;
Nanette,Joyce [30]
;
Erik K,Henricson [31]
;
Ulrike,Schara-Schmidt [31]
;
Andrea,Gangfuss [32]
;
Ekkehard,Wilichowski [33]
;
Richard J,Barohn [34]
;
Jeffrey M,Statland [35]
;
Craig,Campbell [36]
;
Giuseppe,Vita [37]
;
Gian Luca,Vita [38]
;
James F,Howard [39]
;
Imelda,Hughes [40]
;
Hugh J,McMillan [41]
;
Elena,Pegoraro [41]
;
Luca,Bello [42]
;
W Bryan,Burnette [43]
;
Mathula,Thangarajh [44]
;
Taeun,Chang
作者单位：
John Walton Muscular Dystrophy Research Centre, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle upon Tyne, England.
[1]
Department of Neurology, University of Rochester Medical Center, Rochester, New York.;Department of Biostatistics and Computational Biology, University of Rochester Medical Center, Rochester, New York.
[2]
Department of Neurology, University of Rochester Medical Center, Rochester, New York.
[3]
Newcastle University, Newcastle upon Tyne, England.
[4]
Newcastle University, Newcastle upon Tyne, England.;NIHR Clinical Research Network North East and North Cumbria, Newcastle upon Tyne, England.
[5]
Department of Neuropediatrics and Muscle Disorders, Faculty of Medicine, University Hospital Freiburg, Freiburg, Germany.;Department of Neuropediatrics, University Hospital Bonn, Bonn, Germany.
[6]
Ohio State University, Columbus.
[7]
Robert Jones and Agnes Hunt Orthopaedic Hospital, NHS Foundation Trust, Oswestry, England.
[8]
Leeds General Infirmary, Leeds, England.
[9]
David Geffen School of Medicine, University of California, Los Angeles.
[10]
Alderhey Children's Hospital NHS Foundation Trust, Liverpool, England.
[11]
Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy.
[12]
Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy.;Dubowitz Neuromuscular Centre, UCL NIHR GOSH Biomedical Research Centre, UCL Great Ormond Street Institute of Child Health, London, England.
[13]
Department of Pediatric Neurology, University of Utah, Salt Lake City.
[14]
Glasgow Paediatric Neuromuscular Research Centre, Greater Glasgow and Clyde NHS Yorkhill Hospital, Glasgow, Scotland.
[15]
University Hospitals Birmingham NHS Foundation Trust, Birmingham, England.
[16]
Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus, Ohio.
[17]
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois.
[18]
Great Ormond Street Hospital, London, England.
[19]
Department of Neurology, Boston Children's Hospital and Harvard Medical School, Boston, Massachusetts.
[20]
Department of Neurology, Boston Children's Hospital and Harvard Medical School, Boston, Massachusetts.;Paul and Sheila Wellstone Muscular Dystrophy Center and Department of Neurology, University of Minnesota Medical School, Minneapolis.
[21]
Health Sciences Center, University of New Mexico, Albuquerque.
[22]
Cumming School of Medicine, University of Calgary and Alberta Children's Hospital Research Institute, Calgary, Canada.
[23]
Neuromuscular Center, AOU Città della Salute e della Scienza, University of Turin, Turin, Italy.
[24]
Abteilung Neuropädiatrie, Medizinische Fakultät Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.
[25]
Nemours Children's Hospital, Orlando, Florida.;Center for Experimental Neurotherapeutics, St Jude Children's Research Hospital, Memphis, Tennessee.
[26]
Nemours Children's Hospital, Orlando, Florida.
[27]
Penn State Health Milton S. Hershey Medical Center, Hershey, Pennsylvania.;Department of Neurology, School of Medicine, University of Colorado, Aurora.
[28]
Penn State Health Milton S. Hershey Medical Center, Hershey, Pennsylvania.
[29]
Department of Physical Medicine and Rehabilitation and Department of Pediatrics, University of California-Davis, Sacramento.
[30]
Clinic for Pediatrics I, Pediatric Neurology, University Hospital Essen, Essen, Germany.
[31]
Department of Pediatrics and Adolescent Medicine, Division of Pediatric Neurology, University Medical Center Göttingen, Göttingen, Germany.
[32]
University of Missouri, Columbia.
[33]
University of Kansas Medical Center, Kansas City.
[34]
Departments of Pediatrics, Clinical Neurological Sciences, and Epidemiology, University of Western Ontario, London, Canada.
[35]
ERN Neuromuscular Unit, Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy.
[36]
Unit of Neurology, IRCCS Centro Neurolesi Bonino-Pulejo, Messina, Italy.
[37]
School of Medicine, University of North Carolina, Chapel Hill.
[38]
Royal Manchester Children's Hospital, Manchester, England.
[39]
Children's Hospital of Eastern Ontario Research Institute, University of Ottawa, Ottawa, Canada.
[40]
ERN Neuromuscular Unit, Department of Neuroscience, University of Padova, Padua, Italy.
[41]
Vanderbilt University Medical Center, Nashville, Tennessee.
[42]
Department of Neurology, Virginia Commonwealth University, Richmond.
[43]
Children's National Hospital, George Washington University, Washington, DC.
[44]
医学主题词
儿童(Child);儿童, 学龄前(Child, Preschool);女(雌)性(Female);糖皮质激素类(Glucocorticoids);人类(Humans);男(雄)性(Male);肌营养不良, 杜氏(Muscular Dystrophy, Duchenne);泼尼松(Prednisone);孕烯二酮类(Pregnenediones)
DOI
10.1001/jama.2022.4315
PMID
35381069
发布时间
2023-07-26
- 浏览4
JAMA
JAMA
1456-1468页
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