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Safety and preliminary efficacy on cognitive performance and adaptive functionality of epigallocatechin gallate (EGCG) in children with Down syndrome. A randomized phase Ib clinical trial (PERSEUS study).

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第一作者: Cécile,Cieuta-Walti
第一单位: Institut Jérôme Lejeune, Paris, France; Sherbrooke University, Québec, Canada.
作者单位: Institut Jérôme Lejeune, Paris, France; Sherbrooke University, Québec, Canada. [1] Integrative Pharmacology and Systems Neuroscience research group, IMIM-Hospital del Mar Medical Research Institute, Barcelona, Spain. [2] Integrative Pharmacology and Systems Neuroscience research group, IMIM-Hospital del Mar Medical Research Institute, Barcelona, Spain; Department of Statistics and Operations Research, Universitat Politècnica de Catalunya/BarcelonaTECH, Barcelona, Spain. [3] Institut Jérôme Lejeune, Paris, France. [4] Pediatric Sevice, IMIM-Hospital del Mar Medical Research Institute, Barcelona, Spain. [5] Social Pediatrics Division, Hospital Infantil Universitario Niño Jesús, Madrid, Spain. [6] Division of Pediatrics, Hospital Universitario Marqués de Valdecilla - Universidad de Cantabria - Instituto de Investigación Valdecilla (IDIVAL), Santander, Cantabria, Spain. [7] Instituto Hispalense de Pediatría, Sevilla, Spain. [8] Division of Pediatrics, Hospital Universitari Sant Joan de Reus, Tarragona, Spain. [9] Clinical Research Unit, IMIM- Hospital del Mar Medical Research Institute, Barcelona, Spain. [10] Clinical Research Support Unit [HUB·IDIBELL], Clinical Pharmacology Department, Bellvitge University Hospital, Barcelona, Spain; Pharmacology Unit, Department of Pathology and Experimental Therapeutics, School of Medicine and Health Sciences, IDIBELL, University of Barcelona, Barcelona, Spain. [11] Service de Gastro-entérologie-Hépatologie-Nutrition Pédiatriques, Hôpital Necker-Enfants Malades Paris, Paris, France. [12] Unité de Biologie Fonctionnelle et Adaptative (BFA), Laboratoire Processus dégénératifs, Stress et Vieillissement, UMR 8251, CNRS, Université de Paris, Paris, France. [13] UMR 8601 CNRS, Laboratoire de Chimie et Biochimie Pharmacologiques et Toxicologiques, Université de Paris, Paris, France. [14] Centre de Référence Malformations Cardiaques Congénitales Complexes, M3C-Necker, Hôpital Universitaire Necker-Enfants Malades, APHP, Université de Paris, Paris, France. [15] Cellular & Systems Neurobiology, Systems Biology Program. Center for Genomic Regulation, Barcelona, Spain. [16] Sherbrooke University, Québec, Canada; Department of Experimental and Health Sciences, Universitat Pompeu Fabra, Barcelona, Spain. Electronic address: rtorre@imim.es. [17]
DOI 10.1016/j.gim.2022.06.011
PMID 35951014
发布时间 2022-10-29
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Genetics in medicine : official journal of the American College of Medical Genetics

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