Effect of RNS60 in amyotrophic lateral sclerosis: a phase II multicentre, randomized, double-blind, placebo-controlled trial.
第一作者:
Ettore,Beghi
第一单位:
Istituto di Ricerche Farmacologiche Mario Negri IRCCS, Milano, Italy.
作者:
Ettore,Beghi [1]
;
Elisabetta,Pupillo [1]
;
Elisa,Bianchi [1]
;
Valentina,Bonetto [1]
;
Silvia,Luotti [1]
;
Laura,Pasetto [1]
;
Caterina,Bendotti [1]
;
Massimo,Tortarolo [1]
;
Francesca,Sironi [1]
;
Laura,Camporeale [1]
;
Alexander V,Sherman [2]
;
Sabrina,Paganoni [3]
;
Ada,Scognamiglio [4]
;
Fabiola,De Marchi [5]
;
Paolo,Bongioanni [5]
;
Renata,Del Carratore [6]
;
Claudia,Caponnetto [7]
;
Luca,Diamanti [8]
;
Daniele,Martinelli [9]
;
Andrea,Calvo [9]
;
Massimiliano,Filosto [10]
;
Alessandro,Padovani [11]
;
Stefano Cotti,Piccinelli [11]
;
Claudia,Ricci [11]
;
Stefania,Dalla Giacoma [12]
;
Nicoletta,De Angelis [12]
;
Maurizio,Inghilleri [12]
;
Rossella,Spataro [13]
;
Vincenzo,La Bella [14]
;
Giancarlo,Logroscino [14]
;
Christian,Lunetta [15]
;
Claudia,Tarlarini [16]
;
Jessica,Mandrioli [17]
;
Ilaria,Martinelli [17]
;
Cecilia,Simonini [18]
;
Elisabetta,Zucchi [19]
;
Maria Rosaria,Monsurrò [19]
;
Dario,Ricciardi [20]
;
Francesca,Trojsi [19]
;
Nilo,Riva [19]
;
Massimo,Filippi [21]
;
Isabella Laura,Simone [22]
;
Gianni,Sorarù [22]
;
Cristina,Spera [22]
;
Lucia,Florio [23]
;
Sonia,Messina [23]
;
Massimo,Russo [24]
;
Gabriele,Siciliano [25]
;
Amelia,Conte [26]
;
Maria Valeria,Saddi [27]
;
Nicola,Carboni [28]
;
Letizia,Mazzini [28]
;
RNS60-ALS Study Group [29]
作者单位:
Istituto di Ricerche Farmacologiche Mario Negri IRCCS, Milano, Italy.
[1]
Neurological Clinical Research Institute, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA.
[2]
Sean M. Healey and AMG Center for ALS at Mass General Hospital, Department of Neurology, Boston, Massachusetts, USA.
[3]
Spaulding Rehabilitation Hospital, Department of PM&R, Harvard Medical School, Boston, Massachusetts, USA.
[4]
ALS Expert Center 'Maggiore della Carità' Hospital and University of Piemonte Orientale, Novara, Italy.
[5]
Spinal Cord Injuries Section, Azienda Ospedaliero-Universitaria Pisana, Pisa, Italy.
[6]
Institute of Clinical Physiology, CNR-, Pisa, Italy.
[7]
IRCCS Ospedale Policlinico San Martino, Genoa, Italy.
[8]
IRCCS Mondino Foundation, Pavia, Italy.
[9]
Centro Regionale Esperto per la Sclerosi Laterale Amiotrofica, Dipartimento di Neuroscienze 'Rita Levi Montalcini', Università degli Studi di Torino, AOU Città della Salute e della Scienza di Torino, Torino, Italy.
[10]
Department of Clinical and Experimental Sciences, University of Brescia, Gussago Brescia, Italy.
[11]
Department of Medical, Surgical and Neurological Sciences, University of Siena, Siena, Italy.
[12]
Università di Roma 'Sapienza' UOSD Malattie Neurodegenerative, Centro Malattie Rare Neuromuscolari Policlinico Universitario Umberto I, Roma, Italy.
[13]
ALS Clinical Research Center, AOUP 'P Giaccone' - University of Palermo, Palermo, Italy.
[14]
Center for neurodegenerative diseases and the Aging Brain, Department of Clinical Research in Neurology of the University of Bari at 'Pia Fondazione Card G. Panico 'Hospital Tricase, Tricase, Italy.
[15]
Department of Basic Medicine Neuroscience and Sense Organs, University Aldo Moro Bari, Bari, Italy.
[16]
Centro Clinico NeMO Milano, Fondazione Serena ONLUS, Milan, Italy.
[17]
Department of Biomedical, Metabolic and Neural Sciences, University of Modena and Reggio Emilia, Modena, Italy.
[18]
Department of Neurosciences, Azienda Ospedaliero-Universitaria Di Modena, Modena, Italy.
[19]
Clinical and Experimental Medicine PhD Program, University of Modena and Reggio Emilia, Modena, Italy.
[20]
Neuroscience PhD Program, University of Modena and Reggio Emilia, Modena, Italy.
[21]
Department of Advanced Medical and Surgical Sciences, University of Campania 'Luigi Vanvitelli', Naples, Italy.
[22]
Neurology Unit, Neurorehabilitation Unit, and Neurophysiology Unit, Vita-Salute San Raffaele University and San Raffaele Scientific Institute, Milan, Italy.
[23]
Neurology Unit, Department of Basic Medical Sciences, Neurosciences and Sense Organs, University of Bari, Bari, Italy.
[24]
Motor Neuton Disease Center, Department of Neurosciences, Azienda Ospedale Università di Padova, Padova, Italy.
[25]
Azienda Ospedaliera 'S Maria' Terni, Terni, Italy.
[26]
Neurology Department, Fondazione IRCCS Casa Sollievo della Sofferenza, San Giovanni Rotondo, Italy.
[27]
Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy.
[28]
Department of clinical and experimental medicine, University of Pisa, Pisa, Italy.
[29]
Centro Clinico NEMO-Fondazione Policlinico Universitario A. Gemelli IRCCS, Roma, Italy.
[30]
Neurology Department, San Francesco Hospital, Nuoro, Italy.
[31]
主题词
人类(Humans);肌萎缩侧索硬化(Amyotrophic Lateral Sclerosis);生活质量(Quality of Life);神经变性疾病(Neurodegenerative Diseases);双盲法(Double-Blind Method);治疗结果(Treatment Outcome)
DOI
10.1111/ene.15573
PMID
36148821
发布时间
2023-04-15
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European journal of neurology
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