Gene therapy for selected neuromuscular and trinucleotide repeat disorders - An insight to subsume South Asia for multicenter clinical trials.
第一作者:
Nalaka,Wijekoon
第一单位:
Interdisciplinary Centre for Innovations in Biotechnology and Neuroscience, University of Sri Jayewardenepura, Nugegoda, Sri Lanka.;School for Mental Health and Neuroscience, Faculty of Health, Medicine & Life Sciences, Maastricht University, Maastricht, the Netherlands.;EURON - European Graduate School of Neuroscience, the Netherlands.
作者:
关键词
BMD, Becker muscular dystrophyBio BankDMD, Duchenne muscular dystrophyDeveloping CountriesDuchenne Muscular DystrophyEMA, European Medical AgencyEMQN, European Molecular Quality Genetics NetworkFDA, U. S. Food and Drug AdministrationHD, Huntington’s diseaseHIC, High Income CountriesHuntington’s DiseaseIndian Sub-continentMLPA, Multiplex Ligation Dependent Probe AmplificationNeurogenetic DisordersSCA, Spinocerebellar ataxiaSMA, Spinal muscular atrophySpinal Muscular AtrophySpinocerebellar AtaxiaUMIC, Upper Middle Income CountriesWTO, World Trade Organization
DOI
10.1016/j.ibneur.2023.01.009
PMID
36819775
发布时间
2023-02-24
- 浏览1
IBRO neuroscience reports
2023年14卷
146-153页
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