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Longitudinal Assessment of Timed Function Tests in Ambulatory Individuals with SMA Treated with Nusinersen.

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第一作者: Kristin J,Krosschell
第一单位: Department of Physical Therapy and Human Movement Sciences, Northwestern University Feinberg School of Medicine, USA.;Department of Pediatrics, Northwestern University Feinberg School of Medicine, USA.
作者单位: Department of Physical Therapy and Human Movement Sciences, Northwestern University Feinberg School of Medicine, USA.;Department of Pediatrics, Northwestern University Feinberg School of Medicine, USA. [1] Department of Rehabilitation Services, Ann and Robert H. Lurie Children's Hospital of Chicago, USA.;Division of Neurology, Ann and Robert H. Lurie Children's Hospital of Chicago, USA. [2] Biostatistics Collaboration Center, Northwestern University Feinberg School of Medicine, Chicago, IL, USA- sponsor.;Statistical Consulting, OSF Healthcare, Chicago, IL, USA. [3] Chicago College of Osteopathic Medicine, Midwestern University Downers Grove, IL, USA. [4] Graduate Program of Genetic Engineering, Northwestern University, Chicago, IL, USA. [5] Division of Neurology, Ann and Robert H. Lurie Children's Hospital of Chicago, USA. [6] Department of Pediatrics, Northwestern University Feinberg School of Medicine, USA.;Division of Neurology, Ann and Robert H. Lurie Children's Hospital of Chicago, USA. [7] Ultragenyx Pharmaceutical, Inc, USA. [8] Department of Pediatrics, Northwestern University Feinberg School of Medicine, USA.;Stanley Manne Children's Research Institute, Ann and Robert H. Lurie Children's Hospital of Chicago, USA. [9] Department of Pediatrics, Northwestern University Feinberg School of Medicine, USA.;Division of Neurology, Ann and Robert H. Lurie Children's Hospital of Chicago, USA.;Stanley Manne Children's Research Institute, Ann and Robert H. Lurie Children's Hospital of Chicago, USA. [10]
DOI 10.3233/JND-221519
PMID 36872785
发布时间 2023-05-09
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Journal of neuromuscular diseases

Journal of neuromuscular diseases

2023年10卷3期

337-348页

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