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Prime editing-based gene correction alleviates the hyperexcitable phenotype and seizures of a genetic epilepsy mouse model.

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第一作者: Bi-Rong,Cao
第一单位: State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica, Chinese Academy of Sciences, Shanghai, 201203, China.;University of Chinese Academy of Sciences, Beijing, 100049, China.
作者: Bi-Rong,Cao [1] ; Yi-Ming,Huang [2] ; Fu-Yun,Tian [3] ; Jin-Hui,Li [2] ; Chun-Long,Xu [2] ; Yu,Wei [4] ; Ji-Kai,Liu [4] ; Qian-Bei,Guo [5] ; Hai-Yan,Xu [5] ; Li,Zhan [5] ; Rui-Min,Lv [2] ; Yi-di,Sun [6] ; Xin-de,Hu [7] ; Zhao-Bing,Gao [8] ; Chang-Yang,Zhou [9]
作者单位: State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica, Chinese Academy of Sciences, Shanghai, 201203, China.;University of Chinese Academy of Sciences, Beijing, 100049, China. [1] Institute of Neuroscience, CAS Center for Excellence in Brain Science and Intelligence Technology, Chinese Academy of Sciences, Shanghai, 200031, China. [2] State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica, Chinese Academy of Sciences, Shanghai, 201203, China.;Zhongshan Institute for Drug Discovery, Shanghai Institute of Materia Medica, Chinese Academy of Sciences, Zhongshan, 528400, China. [3] Shanghai Immunocan Biotech Co., LTD, Shanghai, 201800, China. [4] State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica, Chinese Academy of Sciences, Shanghai, 201203, China. [5] Institute of Neuroscience, CAS Center for Excellence in Brain Science and Intelligence Technology, Chinese Academy of Sciences, Shanghai, 200031, China. ydsun@ion.ac.cn. [6] Institute of Neuroscience, CAS Center for Excellence in Brain Science and Intelligence Technology, Chinese Academy of Sciences, Shanghai, 200031, China. huxinde@ion.ac.cn. [7] State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica, Chinese Academy of Sciences, Shanghai, 201203, China. zbgao@simm.ac.cn.;University of Chinese Academy of Sciences, Beijing, 100049, China. zbgao@simm.ac.cn.;Zhongshan Institute for Drug Discovery, Shanghai Institute of Materia Medica, Chinese Academy of Sciences, Zhongshan, 528400, China. zbgao@simm.ac.cn. [8] Institute of Neuroscience, CAS Center for Excellence in Brain Science and Intelligence Technology, Chinese Academy of Sciences, Shanghai, 200031, China. zhouchangyang@ion.ac.cn. [9]
DOI 10.1038/s41401-023-01115-5
PMID 37402996
发布时间 2024-11-02
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Acta pharmacologica Sinica

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