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Simoctocog alfa (Nuwiq®) in previously untreated patients with severe haemophilia A-Final efficacy and safety results from the NuProtect study.

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第一作者: Mary,Mathias
第一单位: Haemophilia Comprehensive Care Centre, Great Ormond Street Hospital for Children NHS Trust Haemophilia Centre, NIHR GOSH BRC, London, UK.
作者单位: Haemophilia Comprehensive Care Centre, Great Ormond Street Hospital for Children NHS Trust Haemophilia Centre, NIHR GOSH BRC, London, UK. [1] Department of Hematology, Christian Medical College, Vellore, India. [2] Department of Pediatrics, Division of Hematology/Oncology/BMT, University of British Columbia and British Columbia Children's Hospital, Vancouver, Canada. [3] Department of Paediatrics, Division of Haematology/Oncology and Child Health Evaluative Sciences, Research Institute Hospital for Sick Children, Toronto, Canada. [4] Congenital Coagulopathies Reference Centre, São João University Hospital Centre, Porto, Portugal. [5] AP-HM, Department of Pediatric Hematology Oncology, Children Hospital La Timone, Aix Marseille Univ INSERM, INRA, C2VN, Marseille, France. [6] Department of Pediatrics, McMaster Centre of Transfusion Research, McMaster University, Hamilton, Canada. [7] Department of Paediatrics, Western Ukrainian Specialized Children's Medical Centre, Lviv, Ukraine. [8] Department of Pediatrics, University of California Davis Medical Center, Sacramento, California, USA. [9] Department of Paediatric Haematology and Oncology, Addenbrooke's Hospital, Cambridge University Hospital NHS Foundation Trust, Cambridge, UK. [10] Department of Medicine and Surgery, University of Perugia, Perugia, Italy. [11] Centre Régional de Traitement de l'Hémophilie, Hôpital Trousseau, Tours, France. [12] Haemophilia Treatment Centre, Univ Rennes, CHU Rennes, INSERM, EHESP, Irset (Institut de Recherche en Santé, Environnement et Travail) - UMR_S 1085, Rennes, France. [13] Servicio de Hematología, Hospital Univeristario La Paz, Autónoma, University of Madrid, Madrid, Spain. [14] Department of Haematooncology, Division of Paediatrics, University Medical Center Ljubljana, Ljubljana, Slovenia. [15] Haemostasis Group of the Polish Society of Haematology and Transfusiology, Warsaw, Poland. [16] Department of Hematology, Sahyadri Speciality Hospital, Pune, India. [17] Center for Thrombosis and Hemorrhagic Diseases, IRCCS Humanitas Research Hospital, Milan, Italy. [18] Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn, Bonn, Germany. [19] Regional Reference Centre for Inherited Bleeding and Thrombotic Disorders, Regina Margherita Children Hospital, Turin, Italy. [20] Centre Régional de Traitement de I'Hémophilie, University Hospital of Nantes, Nantes, France. [21] Department of Hematology, OHMATDYT - National Specialized Children's Hospital, Kiev, Ukraine. [22] Octapharma Pharmazeutika Produktionsges m.b.H, Vienna, Austria. [23] Octapharma AG, Lachen, Switzerland. [24] Department of Hematology, St. Jude Children's Research Hospital, Memphis, Tennessee, USA. [25]
DOI 10.1111/ejh.14040
PMID 37439123
发布时间 2023-09-18
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European journal of haematology

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