作者:
Kevin A,Strauss [1]
;
Vincent J,Carson [2]
;
Emilienne,Bolettieri [3]
;
Mariah,Everett [3]
;
Ashton,Bollinger [3]
;
Lauren E,Bowser [3]
;
Keturah,Beiler [3]
;
Millie,Young [3]
;
Simon,Edvardson [4]
;
Nitay,Fraenkel [4]
;
Adele,D'Amico [5]
;
Enrico,Bertini [5]
;
Lokesh,Lingappa [6]
;
Devyani,Chowdhury [7]
;
Linda P,Lowes [8]
;
Megan,Iammarino [8]
;
Lindsay N,Alfano [8]
;
Karlla W,Brigatti [3]
作者单位:
Clinic for Special Children, Strasburg, Pennsylvania, USA.;Department of Pediatrics, Penn Medicine-Lancaster General Hospital, Pennsylvania, Lancaster, USA.;Department of Pediatrics, UMass Chan Medical School, Worcester, Massachusetts, USA.;Department of Molecular, Cell & Cancer Biology, UMass Chan Medical School, Worcester, Massachusetts, USA.
[1]
Clinic for Special Children, Strasburg, Pennsylvania, USA.;Department of Pediatrics, Penn Medicine-Lancaster General Hospital, Pennsylvania, Lancaster, USA.
[2]
Clinic for Special Children, Strasburg, Pennsylvania, USA.
[3]
ALYN Hospital Pediatric and Adolescent Rehabilitation Center, Jerusalem, Israel.
[4]
Unit of Muscular and Neurodegenerative Disorders, Department of Neurosciences, IRCCS Bambino Gesù Children's Hospital, Rome, Italy.
[5]
Department of Pediatric Neurology, Rainbow Children's Hospital, Hyderabad, India.
[6]
Cardiology Care for Children, Lancaster, Pennsylvania, USA.;Department of Cardiology, Nemours Children's Health, Wilmington, Delaware, USA.
[7]
Center for Gene Therapy, Nationwide Children's Hospital, Columbus, Ohio, USA.
[8]
DOI
10.1002/acn3.51884
PMID
37632133
发布时间
2024-11-12