Effects of tofersen treatment in patients with <i>SOD1</i>-ALS in a "real-world" setting - a 12-month multicenter cohort study from the German early access program.
第一作者:
Maximilian,Wiesenfarth
第一单位:
Department of Neurology, Ulm University, 89081, Ulm, Germany.
作者:
Maximilian,Wiesenfarth [1]
;
Johannes,Dorst [2]
;
David,Brenner [1]
;
Zeynep,Elmas [1]
;
Özlem,Parlak [1]
;
Zeljko,Uzelac [1]
;
Katharina,Kandler [1]
;
Kristina,Mayer [1]
;
Ulrike,Weiland [1]
;
Christine,Herrmann [1]
;
Joachim,Schuster [2]
;
Axel,Freischmidt [1]
;
Kathrin,Müller [3]
;
Reiner,Siebert [4]
;
Franziska,Bachhuber [1]
;
Tatiana,Simak [1]
;
Kornelia,Günther [1]
;
Elke,Fröhlich [1]
;
Antje,Knehr [1]
;
Martin,Regensburger [5]
;
Alexander,German [6]
;
Susanne,Petri [7]
;
Julian,Grosskreutz [8]
;
Thomas,Klopstock [9]
;
Peter,Reilich [10]
;
Florian,Schöberl [10]
;
Tim,Hagenacker [11]
;
Ute,Weyen [12]
;
René,Günther [13]
;
Maximilian,Vidovic [14]
;
Martin,Jentsch [15]
;
Thomas,Haarmeier [15]
;
Patrick,Weydt [16]
;
Ivan,Valkadinov [17]
;
Jasper,Hesebeck-Brinckmann [17]
;
Julian,Conrad [17]
;
Jochen Hans,Weishaupt [17]
;
Peggy,Schumann [18]
;
Peter,Körtvélyessy [19]
;
Thomas,Meyer [20]
;
Wolfgang Philipp,Ruf [1]
;
Simon,Witzel [1]
;
Makbule,Senel [1]
;
Hayrettin,Tumani [2]
;
Albert Christian,Ludolph [2]
作者单位:
Department of Neurology, Ulm University, 89081, Ulm, Germany.
[1]
Department of Neurology, Ulm University, 89081, Ulm, Germany.;German Centre for Neurodegenerative Diseases (DZNE) Site Ulm, 89081, Ulm, Germany.
[2]
Department of Neurology, Ulm University, 89081, Ulm, Germany.;Institute of Human Genetics, Ulm University and Ulm University Medical Center, 89081, Ulm, Germany.
[3]
Institute of Human Genetics, Ulm University and Ulm University Medical Center, 89081, Ulm, Germany.
[4]
Department of Molecular Neurology, Friedrich-Alexander-Universität Erlangen-Nürnberg (FAU), 91054, Erlangen, Germany.;Deutsches Zentrum Immuntherapie (DZI), University Hospital Erlangen, 91054, Erlangen, Germany.
[5]
Department of Molecular Neurology, Friedrich-Alexander-Universität Erlangen-Nürnberg (FAU), 91054, Erlangen, Germany.
[6]
Department of Neurology, Hannover Medical School, 30625, Hannover, Germany.
[7]
Precision Neurology of Neuromuscular and Motoneuron Diseases, University of Lübeck, 23538, Lübeck, Germany.
[8]
Department of Neurology with Friedrich-Baur-Institute, LMU University Hospital, LMU Munich, 80336, München, Germany.;German Centre for Neurodegenerative Diseases (DZNE) Site Munich, 81377, Munich, Germany.;Munich Cluster for Systems Neurology (SyNergy), 81377, Munich, Germany.
[9]
Department of Neurology with Friedrich-Baur-Institute, LMU University Hospital, LMU Munich, 80336, München, Germany.
[10]
Department of Neurology and Center for Translational Neuro and Behavioral Sciences (C-TNBS), University Hospital Essen, 45127, Essen, Germany.
[11]
Department of Neurology, Ruhr-University Bochum, BG-Kliniken Bergmannsheil, 44789, Bochum, Germany.
[12]
Department of Neurology, University Hospital Carl Gustav Carus, Technische Universität Dresden, 01307, Dresden, Germany.;German Center for Neurodegenerative Diseases (DZNE) Site Dresden, 01307, Dresden, Germany.
[13]
Department of Neurology, University Hospital Carl Gustav Carus, Technische Universität Dresden, 01307, Dresden, Germany.
[14]
Department of Neurology, Helios Klinikum Krefeld, 47805, Krefeld, Germany.
[15]
Department for Neurodegenerative Disorders and Gerontopsychiatry, Bonn University, 53127, Bonn, Germany.;German Centre for Neurodegenerative Diseases (DZNE) Site Bonn, 53127, Bonn, Germany.
[16]
Division for Neurodegenerative Diseases, Neurology Department, Mannheim Center for Translational Medicine, University Medicine Mannheim, Heidelberg University, 68167, Mannheim, Germany.
[17]
Ambulanzpartner Soziotechnologie GmbH, 13353, Berlin, Germany.
[18]
Department of Neurology, Center for ALS and Other Motor Neuron Disorders, Charité - Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin, Humboldt-Universität zu Berlin, and Berlin Institute of Health, 13353, Berlin, Germany.;German Centre for Neurodegenerative Diseases (DZNE) Site Magdeburg, 39120, Magdeburg, Germany.
[19]
Department of Neurology, Center for ALS and Other Motor Neuron Disorders, Charité - Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin, Humboldt-Universität zu Berlin, and Berlin Institute of Health, 13353, Berlin, Germany.
[20]
DOI
10.1016/j.eclinm.2024.102495
PMID
38384337
发布时间
2024-02-24
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2024年69卷
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