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A phase 3 randomized trial of mavorixafor, a CXCR4 antagonist, for WHIM syndrome.

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作者单位: Department of Clinical and Experimental Sciences, University of Brescia and ASST Spedali Civili, Brescia, Italy. [1] Pediatric Allergy and Clinical Immunology Department, Clinical Immunology and Primary Immunodeficiencies Unit, Hospital Sant Joan de Déu, Barcelona, Spain.;Department of Surgery and Surgical Specializations, Facultat de Medicina i Ciències de la Salut, Universitat de Barcelona, Barcelona, Spain.;Institut de Recerca Sant Joan de Déu, Barcelona, Spain. [2] Division of Allergy and Clinical Immunology, Johns Hopkins University, Baltimore, MD. [3] Pediatric Hematology and Oncology Institute, Hospices Civils de Lyon and Claude Bernard University, Lyon, France. [4] University of Washington Medical Center, Seattle, WA. [5] The University of Texas Southwestern Medical Center, Dallas, TX. [6] California Dermatology Institute, Thousand Oaks, CA. [7] Department of Paediatrics, Aarhus University Hospital, Aarhus, Denmark. [8] Department of Pediatrics, Seoul National University College of Medicine, Seoul National University Cancer Research Institute, Seoul National University Children's Hospital, Seoul, South Korea. [9] Department of Immunology, Royal Free London NHS Foundation Trust, London, United Kingdom. [10] Department of Pediatric Immunology, Rheumatology and Infectious Disease, Emma Children's Hospital, Amsterdam University Medical Centers, Amsterdam, The Netherlands. [11] RM Gorbacheva Research Institute, Pavlov University, St. Petersburg, Russia. [12] Immunology Department, Sullivan Nicolaides Pathology Auchenflower, Wesley Medical Center, Auchenflower, QLD, Australia. [13] Pediatric Hematology Unit, Emek Medical Center, Afula, Israel.;The Ruth and Bruce Rappaport Faculty of Medicine, Technion, Israel Institute of Technology, Haifa, Israel. [14] Paediatric Infectious Disease, Rheumatology and Immunology Unit, Hospital Universitario Virgen del Rocío, Instituto de Biomedicina de Sevilla, IBiS/Universidad de Sevilla/CSIC, Red de Investigación Translacional en Infectología Pediátrica RITIP, Seville, Spain. [15] Paediatric Infectious Disease, Rheumatology and Immunology Unit, Hospital Universitario Virgen del Rocío, Instituto de Biomedicina de Sevilla, IBiS/Universidad de Sevilla/CSIC, Red de Investigación Translacional en Infectología Pediátrica RITIP, Seville, Spain.;Departmento de Pediatría, Facultad de Medicina, Universidad de Sevilla, Seville, Spain. [16] Queensland Children's Hospital, South Brisbane, QLD, Australia. [17] Dmitry Rogachev National Medical Research Center of Pediatric Hematology, Oncology and Immunology, Moscow, Russia. [18] Department of Hematology, Amsterdam University Medical Centers, Amsterdam, The Netherlands. [19] Division of Rheumatology and Immunology, Department of Medicine, Duke University, Durham, NC. [20] Division of Infectious Diseases and Tropical Medicine, Department of Internal Medicine I, Medical University of Vienna, Vienna, Austria. [21] X4 Pharmaceuticals, Boston, MA. [22] Centre de Référence des Neutropénies Chroniques, Assistance Publique-Hôpitaux de Paris Sorbonne Université-Hôpital d'Enfants Armand-Trousseau, Paris, France. [23]
DOI 10.1182/blood.2023022658
PMID 38643510
发布时间 2024-11-04
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