Non-viral DNA delivery and TALEN editing correct the sickle cell mutation in hematopoietic stem cells.

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作者： Arianna,Moiani ^[1] ; Gil,Letort ^[2] ; Sabrina,Lizot ^[2] ; Anne,Chalumeau ^[3] ; Chloe,Foray ^[2] ; Tristan,Felix ^[3] ; Diane,Le Clerre ^[2] ; Sonal,Temburni-Blake ^[4] ; Patrick,Hong ^[4] ; Sophie,Leduc ^[2] ; Noemie,Pinard ^[2] ; Alan,Marechal ^[2] ; Eduardo,Seclen ^[4] ; Alex,Boyne ^[4] ; Louisa,Mayer ^[4] ; Robert,Hong ^[4] ; Sylvain,Pulicani ^[2] ; Roman,Galetto ^[2] ; Agnès,Gouble ^[2] ; Marina,Cavazzana ^[5] ; Alexandre,Juillerat ^[6] ; Annarita,Miccio ^[7] ; Aymeric,Duclert ^[4] ; Philippe,Duchateau ^[3] ; Julien,Valton ^[2]

作者单位： Cellectis S.A., 8 Rue de la Croix Jarry, Paris, France. arianna.moiani@cellectis.com. ^[1] Cellectis S.A., 8 Rue de la Croix Jarry, Paris, France. ^[2] Université Paris Cité, Imagine Institute, Laboratory of Chromatin and Gene Regulation During Development, INSERM UMR 1163, Paris, France. ^[3] Cellectis Inc., 430 East 29th Street, New York, NY, USA. ^[4] Biotherapy Clinical Investigation Center, Necker Children's Hospital, Assistance Publique Hopitaux de Paris, Paris, France. ^[5] Human Lymphohematopoiesis Laboratory, Imagine Institute, INSERM UMR1163, Paris Cité University, Paris, France. ^[6] Biotherapy Department, Necker Children's Hospital, Assistance Publique Hopitaux de Paris, Paris, France. ^[7] Cellectis S.A., 8 Rue de la Croix Jarry, Paris, France. julien.valton@cellectis.com. ^[8]