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Reported Adverse Events in a Multicenter Cohort of Patients Ages 6-18 Years with Cystic Fibrosis and at Least One F508del Allele Receiving Elexacaftor/Tezacaftor/Ivacaftor.

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作者单位: Department of Pediatric Medicine, Meyer Children's Hospital IRCCS, Cystic Fibrosis Regional Reference Center, Florence, Italy. Electronic address: vito.terlizzi@meyer.it. [1] Department of Pediatric Medicine, Meyer Children's Hospital IRCCS, Cystic Fibrosis Regional Reference Center, Florence, Italy. [2] Pediatric Respiratory Unit, Department of Clinical and Experimental Medicine, San Marco Hospital, University of Catania, Catania, Italy. [3] Department of Pediatric Medicine, Meyer Children's Hospital IRCCS, Cystic Fibrosis Regional Reference Center, Florence, Italy; SC di Pneumologia e UTSIR, AORN Santobono-Pausilipon, Naples, Italy; Paediatric Unit, Department of Translational Medical Sciences, Cystic Fibrosis Regional Reference Center, University of Naples Federico II, Naples, Italy. [4] Department of Pathophysiology and Transplantation, Cystic Fibrosis Regional Reference Center, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, University of Milan, Milan, Italy. [5] Paediatric Unit, Department of Translational Medical Sciences, Cystic Fibrosis Regional Reference Center, University of Naples Federico II, Naples, Italy. [6] Cystic Fibrosis Centre, Bambino Gesù Children's Hospital, IRCCS, Rome, Italy. [7] Department of Pediatrics, IRCCS Institute "Giannina Gaslini", Cystic Fibrosis Centre, Genoa, Italy. [8] Paediatric Pulmonology Unit, Regina Margherita Hospital AOU Città della Salute e della Scienza, Torino, Italy. [9] Cystic Fibrosis Support Center, Ospedale G. Tatarella di Cerignola, Cerignola, Italy. [10] Department of Pediatrics, Cystic Fibrosis Regional Support Center, ASST Spedali Civili Brescia, University of Brescia, Brescia, Italy. [11] Lazio Reference Center for Cystic Fibrosis, Policlinico Umberto I University Hospital, Sapienza University, Rome, Italy. [12] Cystic Fibrosis Center, Ospedale Giovanni Di Cristina, Palermo, Italy. [13] U.O.S.D. C.R.R. Fibrosi Cistica Ospedale "San Liberatore" di Atri-Dipartimento Materno Infantile-ASL Teramo, Teramo, Italy. [14] Pediatric Gastroenterology and Cystic Fibrosis Unit, Policlinico G. Martino Hospital, University of Messina, Messina, Italy. [15] Pediatric Cystic Fibrosis Centre, Azienda Universitaria Ospedaliera Consorziale Policlinico, Bari, Italy. [16] Cystic Fibrosis Center of Umbria Region, Branca Hospital, Branca, Italy. [17] Freelance Statistician, Milan, Italy. [18] Cystic Fibrosis Center, Hospital San Carlo, Potenza, Italy. [19]
DOI 10.1016/j.jpeds.2024.114176
PMID 38945446
发布时间 2024-10-23
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