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Fast and facile synthesis of amidine-incorporated degradable lipids for versatile mRNA delivery in vivo.

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第一作者: Xuexiang,Han
第一单位: Department of Bioengineering, University of Pennsylvania, Philadelphia, PA, USA.;Key Laboratory of RNA Innovation, Science and Engineering, CAS Center for Excellence in Molecular Cell Science, Shanghai Institute of Biochemistry and Cell Biology, Chinese Academy of Sciences, University of Chinese Academy of Sciences, Shanghai, China.
作者单位: Department of Bioengineering, University of Pennsylvania, Philadelphia, PA, USA.;Key Laboratory of RNA Innovation, Science and Engineering, CAS Center for Excellence in Molecular Cell Science, Shanghai Institute of Biochemistry and Cell Biology, Chinese Academy of Sciences, University of Chinese Academy of Sciences, Shanghai, China. [1] Department of Medicine, University of Pennsylvania, Philadelphia, PA, USA.;Penn Institute for RNA Innovation, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA.;Department of Bioengineering, George Mason University, Fairfax, VA, USA. [2] Department of Bioengineering, University of Pennsylvania, Philadelphia, PA, USA. [3] Department of Medicine, University of Pennsylvania, Philadelphia, PA, USA. [4] Department of Biomedical Sciences, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, PA, USA. [5] Gene Therapy Program, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. [6] Department of Bioengineering, University of Pennsylvania, Philadelphia, PA, USA.;Department of Medicine, University of Pennsylvania, Philadelphia, PA, USA. [7] Department of Chemistry, Case Western Reserve University, Cleveland, OH, USA. [8] Department of Medicine, University of Pennsylvania, Philadelphia, PA, USA. dreww@upenn.edu.;Penn Institute for RNA Innovation, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. dreww@upenn.edu. [9] Department of Bioengineering, University of Pennsylvania, Philadelphia, PA, USA. mjmitch@seas.upenn.edu.;Penn Institute for RNA Innovation, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. mjmitch@seas.upenn.edu.;Abramson Cancer Center, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. mjmitch@seas.upenn.edu.;Institute for Immunology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. mjmitch@seas.upenn.edu.;Cardiovascular Institute, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. mjmitch@seas.upenn.edu.;Institute for Regenerative Medicine, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. mjmitch@seas.upenn.edu.;Center for Cellular Immunotherapies, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. mjmitch@seas.upenn.edu.;Center for Precision Engineering for Health, University of Pennsylvania, Philadelphia, PA, USA. mjmitch@seas.upenn.edu. [10]
DOI 10.1038/s41557-024-01557-2
PMID 38982196
发布时间 2024-12-10
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