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Invasive procedures and surgery following etranacogene dezaparvovec gene therapy in people with hemophilia B.

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第一作者: Niamh,O'Connell
第一单位: National Coagulation Centre, St. James's Hospital, Dublin, Ireland; School of Medicine, Trinity College, Dublin, Ireland. Electronic address: noconnell@stjames.ie.
作者单位: National Coagulation Centre, St. James's Hospital, Dublin, Ireland; School of Medicine, Trinity College, Dublin, Ireland. Electronic address: noconnell@stjames.ie. [1] Van Creveldkliniek, Department of Benign Hematology, University Medical Center Utrecht, Utrecht University, Utrecht, The Netherlands. [2] CSL Behring, King of Prussia, Pennsylvania, USA. [3] The Center for Inherited Blood Disorders, Orange, California, USA. [4] Department of Pediatrics, Hematology and Oncology, Arkansas Children's Hospital, Little Rock, Arkansas, USA. [5] Department of Vascular Medicine, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam, The Netherlands; Amsterdam Cardiovascular Sciences, Pulmonary Hypertension & Thrombosis, Amsterdam, The Netherlands. [6] Pediatric Hematology-Oncology, University of Utah and Primary Children's Hospital, Salt Lake City, Utah, USA. [7] Center for Bleeding Disorders and Coagulation, Careggi University Hospital, Florence, Italy. [8] Internal Medicine - Angiology and Hemostaseology, Vivantes Klinikum, Berlin, Germany. [9] Cambridge University Hospitals, Cambridge, United Kingdom. [10] Orthopaedic Hemophilia Treatment Center, Los Angeles, California, USA. [11] Department of Hematology, Rigshospitalet, Copenhagen, Denmark. [12]
DOI 10.1016/j.jtha.2024.08.027
PMID 39341368
发布时间 2025-06-06
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Journal of thrombosis and haemostasis : JTH

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