首页> European journal of pediatrics> Respiratory outcomes of onasemnogene abeparvovec treatment for spinal muscular atrophy: national real-world cohort study.

Respiratory outcomes of onasemnogene abeparvovec treatment for spinal muscular atrophy: national real-world cohort study.

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第一作者： Moran,Lavie

第一单位： Pediatric Pulmonology Unit, Dana-Dwek Children's Hospital, Tel Aviv Sourasky Medical Center, Tel Aviv, Israel. moranla@tlvmc.gov.il.;Faculty of Medical and Health Sciences, Tel Aviv University, Tel Aviv, Israel. moranla@tlvmc.gov.il.

作者： Moran,Lavie ^[1] ; Mika,Rochman ^[2] ; Keren,Armoni Domany ^[3] ; Inbal,Golan Tripto ^[4] ; Moria,Be'er ^[2] ; Omri,Besor ^[5] ; Liora,Sagi ^[6] ; Sharon,Aharoni ^[7] ; Mira,Ginsberg ^[8] ; Iris,Noyman ^[9] ; Hagit,Levine ^[10]

作者单位： Pediatric Pulmonology Unit, Dana-Dwek Children's Hospital, Tel Aviv Sourasky Medical Center, Tel Aviv, Israel. moranla@tlvmc.gov.il.;Faculty of Medical and Health Sciences, Tel Aviv University, Tel Aviv, Israel. moranla@tlvmc.gov.il. ^[1] Pediatric Pulmonology Unit, Dana-Dwek Children's Hospital, Tel Aviv Sourasky Medical Center, Tel Aviv, Israel.;Faculty of Medical and Health Sciences, Tel Aviv University, Tel Aviv, Israel. ^[2] Faculty of Medical and Health Sciences, Tel Aviv University, Tel Aviv, Israel.;Pediatric Pulmonology Unit, Sylvan Adams Children's Hospital, E. Wolfson Medical Center, Holon, Israel. ^[3] Pediatric Pulmonary Unit, Soroka University Medical Center, Ben-Gurion University of the Negev, Beer-Sheba, Israel. ^[4] Pediatric Pulmonology Unit, Dana-Dwek Children's Hospital, Tel Aviv Sourasky Medical Center, Tel Aviv, Israel.;Department of Family Medicine, Maccabi Healthcare Services, Tel Aviv, Israel. ^[5] Faculty of Medical and Health Sciences, Tel Aviv University, Tel Aviv, Israel.;Pediatric Neurology Unit, Dana-Dwek Children's Hospital, Tel Aviv Sourasky Medical Center, Tel Aviv, Israel. ^[6] Faculty of Medical and Health Sciences, Tel Aviv University, Tel Aviv, Israel.;Neurology Institute, Schneider Children's Medical Center, Petah-Tikva, Israel. ^[7] Faculty of Medical and Health Sciences, Tel Aviv University, Tel Aviv, Israel.;Department of Pediatric Neurology, Wolfson Medical Center, Holon, Israel. ^[8] Pediatric Neurology Unit, Soroka University Medical Center, Ben-Gurion University of the Negev, Beer-Sheba, Israel. ^[9] Faculty of Medical and Health Sciences, Tel Aviv University, Tel Aviv, Israel.;Pulmonary Institute, Schneider Children's Medical Center, Petah-Tikva, Israel. ^[10]

关键词 Nusinersen Onasemnogene abeparvovec Respiratory Restrictive lung disease Spinal muscular atrophy