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Radiographic and visual response to the type II RAF inhibitor tovorafenib in children with relapsed/refractory optic pathway glioma in the FIREFLY-1 trial.

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第一作者: Karsten,Nysom
第一单位: Department of Pediatrics and Adolescent Medicine, Copenhagen University Hospital, Rigshospitalet, Copenhagen, Capital Region of Denmark, Denmark.
作者单位: Department of Pediatrics and Adolescent Medicine, Copenhagen University Hospital, Rigshospitalet, Copenhagen, Capital Region of Denmark, Denmark. [1] Children's National Hospital, Washington, District of Columbia, USA. [2] Cancer and Blood Disorders Center, Seattle Children's Hospital, Seattle, Washington, USA. [3] Department of Pediatrics, Duke University, Durham, North Carolina, USA. [4] Princess Máxima Center for Pediatric Oncology, Utrecht, The Netherlands. [5] CHU Sainte-Justine, Université de Montréal, Montreal, Quebec, Canada. [6] National Center for Tumor Diseases (NCT), Heidelberg, Germany.;German Cancer Consortium (DKTK), Heidelberg, Germany.;Department of Pediatric Oncology, Hematology, Immunology and Pulmonology, Heidelberg University Hospital, Heidelberg, Germany.;Clinical Cooperation Unit Pediatric Oncology, German Cancer Research Center (DKFZ), Heidelberg, Germany.;Hopp Children's Cancer Center Heidelberg (KiTZ), Heidelberg, Germany. [7] School of Clinical Medicine, University of New South Wales, Sydney, New South Wales, Australia.;Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, New South Wales, Australia.;Kids Cancer Centre, Sydney Children's Hospital, Randwick, New South Wales, Australia. [8] Department of Pediatric Oncology/Hematology, Charité-Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin and Humboldt-Universität Berlin, German HIT-LOGGIC-Registry for LGG in Children and Adolescents, Pediatric Neurooncology Program, Berlin, Germany. [9] Department of Pediatrics, C.S. Mott Children's Hospital, University of Michigan Medical School, Ann Arbor, Michigan, USA. [10] Texas Children's Cancer Center, Texas Children's Hospital, Baylor College of Medicine, Houston, Texas, USA. [11] Primary Children's Hospital and University of Utah, Salt Lake City, Utah, USA. [12] Division of Oncology, Department of Pediatrics, Children's Hospital of Philadelphia, University of Pennsylvania Perelman School of Medicine, Philadelphia, Pennsylvania, USA. [13] NYU Langone Health, New York, New York, USA. [14] Department of Pediatrics, McGill University Health Centre (MUHC), The Montreal Children's Hospital (MCH), Montréal, Quebec, Canada. [15] Great North Children's Hospital and Newcastle University Centre for Cancer, Newcastle-upon-Tyne, UK. [16] Sydney Children's Hospitals Network, Westmead, New South Wales, Australia. [17] South Australian Immunogenomics Cancer Institute, University of Adelaide, Adelaide, Australia.;South Australia Health and Medical Research Institute, Adelaide, South Australia, Australia.;Michael Rice Centre for Hematology and Oncology, Women's and Children's Hospital, Adelaide, South Australia, Australia. [18] Children's Cancer Centre, The Royal Children's Hospital Melbourne, Melbourne, Victoria, Australia. [19] Brain Tumor Research Program, Telethon Kids Cancer Centre, Telethon Kids Institute, University of Western Australia, Perth, Washington, Australia.;Department of Pediatric and Adolescent Oncology and Hematology, Perth Children's Hospital, Perth, Western Australia, Australia. [20] Children's Health Queensland Hospital and Health Service, South Brisbane, Australia. [21] Severance Hospital, Yonsei University Health System, Seoul, Republic of Korea. [22] Pediatric Hemato-Oncology Department, Sheba Medical Center, Ramat Gan, Tel Aviv District, Israel. [23] Pediatric Neuro-Oncology, Dana-Farber/Boston Children's Cancer and Blood Disorders Center, Boston, Massachusetts, USA. [24] Day One Biopharmaceuticals, Brisbane, California, USA. [25] UCL Great Ormond Street Institute of Child Health and Great Ormond Street Hospital for Children, London, UK. [26]
DOI 10.1093/neuonc/noae274
PMID 39700439
发布时间 2025-07-22
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