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Virus-free CRISPR knockin of a chimeric antigen receptor into KLRC1 generates potent GD2-specific natural killer cells.

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第一作者: Keerthana,Shankar
第一单位: Department of Biomedical Engineering, University of Wisconsin-Madison, Madison, WI 53715, USA; Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI 53715, USA.
作者单位: Department of Biomedical Engineering, University of Wisconsin-Madison, Madison, WI 53715, USA; Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI 53715, USA. [1] Department of Biomedical Engineering, University of Wisconsin-Madison, Madison, WI 53715, USA. [2] Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI 53715, USA. [3] Department of Biomedical Engineering, University of Wisconsin-Madison, Madison, WI 53715, USA; Department of Dermatology, University of Wisconsin-Madison, Madison, WI 53715, USA; Carbone Cancer Center, University of Wisconsin-Madison, Madison, WI 53715, USA. [4] Department of Pediatrics, University of Wisconsin School of Medicine and Public Health, Madison, WI 53715, USA; Carbone Cancer Center, University of Wisconsin-Madison, Madison, WI 53715, USA. [5] Department of Hematology, St Jude Children's Research Hospital, Memphis, TN 38105, USA. [6] Center for Human Genomics and Precision Medicine, University of Wisconsin-Madison, Madison, WI 53705, USA. [7] Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI 53715, USA; Department of Pathobiological Sciences, University of Wisconsin-Madison, Madison, WI 53706, USA. [8] Center for Human Genomics and Precision Medicine, University of Wisconsin-Madison, Madison, WI 53705, USA; Department of Surgery, University of Wisconsin-Madison, Madison, WI 53792, USA. [9] Department of Dermatology, University of Wisconsin-Madison, Madison, WI 53715, USA; Department of Pediatrics, University of Wisconsin School of Medicine and Public Health, Madison, WI 53715, USA. [10] Department of Biomedical Engineering, University of Wisconsin-Madison, Madison, WI 53715, USA; Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI 53715, USA; Department of Pediatrics, University of Wisconsin School of Medicine and Public Health, Madison, WI 53715, USA. Electronic address: ksaha@wisc.edu. [11]
DOI 10.1016/j.ymthe.2025.01.024
PMID 39815622
发布时间 2025-07-23
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Molecular therapy : the journal of the American Society of Gene Therapy

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