Real-World Efficacy Profile of Compassionate Use of Asciminib in an Italian, Multi-Resistant Chronic-Phase Chronic Myeloid Leukemia (CML-CP) Patient Population.
第一作者:
Massimo,Breccia
第一单位:
Division of Hematology, Department of Translational and Precision Medicine, Azienda Policlinico Umberto I, Sapienza University, Rome, Italy.
作者:
Massimo,Breccia [1]
;
Antonella Russo,Rossi [2]
;
Valentina,Giai [3]
;
Bruno,Martino [4]
;
Carmen,Fava [5]
;
Mario,Annunziata [6]
;
Elisabetta,Abruzzese [7]
;
Gianni,Binotto [8]
;
Claudia,Baratè [9]
;
Aurelio Pio,Nardozza [10]
;
Alessandra,Misto [10]
;
Paola,Coco [10]
;
Valeria,Calafiore [11]
;
Maria Cristina,Carraro [12]
;
Federica,Cattina [13]
;
Francesco,Cavazzini [14]
;
Maria Teresa,Corsetti [15]
;
Lara,Crucitti [16]
;
Monica,Crugnola [17]
;
Ambra,Di Veroli [18]
;
Paolo,Ditonno [19]
;
Anna,Ermacora [20]
;
Felicetto,Ferrara [21]
;
Angelo,Genua [22]
;
Antonella,Gozzini [23]
;
Stefana,Impera [24]
;
Alessandra,Iurlo [25]
;
Luciano,Levato [26]
;
Luigia,Luciano [27]
;
Maria Cristina,Miggiano [28]
;
Marco,De Gobbi [29]
;
Marco,Santoro [30]
;
Barbara,Scappini [31]
;
Anna Rita,Scortechini [32]
;
Andrea,Patriarca [33]
;
Serena,Rosati [34]
;
Sabina,Russo [35]
;
Rosaria,Sancetta [36]
;
Grazia,Sanpaolo [37]
;
Teresa Maria,Santeramo [38]
;
Silvia,Sibilla [39]
;
Federica,Sorà [40]
;
Paolo,Sportoletti [41]
;
Fabio,Stagno [42]
;
Elena,Trabacchi [43]
;
Fausto,Castagnetti [44]
作者单位:
Division of Hematology, Department of Translational and Precision Medicine, Azienda Policlinico Umberto I, Sapienza University, Rome, Italy.
[1]
Hematology and Transplantation Unit, University of Bari, Bari, Italy.
[2]
Division of Haematology, A.O.U. Città della Salute e della Scienza, Turin, Italy.
[3]
Division of Hematology, Azienda Ospedaliera "Bianchi Melacrino Morelli", Reggio Calabria, Italy.
[4]
Department of Clinical and Biological Sciences, University of Turin, Turin, Italy.
[5]
Hematology Unit, Cardarelli Hospital, Napoli, Italy.
[6]
Hematology Unit, S. Eugenio Hospital, ASL Roma2, Tor Vergata University, Rome, Italy.
[7]
Department of Medicine, Unit of Hematology and Clinical Immunology, University of Padova, Padova, Italy.
[8]
Department of Clinical and Experimental Medicine, UO Hematology, Azienda Ospedaliero Universitaria Pisana, University of Pisa, Pisa, Italy.
[9]
Medical Department, Novartis, Novartis Farma SpA, Milan, Italy.
[10]
U.O. Oncoematologia, A.O.R. Villa Sofia - Vincenzo Cervello, Palermo, Italy.
[11]
UOC Hematology and Transfusion Medicine, Ospedale Luigi Sacco, Milan, Italy.
[12]
Oncology Unit, Hospital Crema, Crema, Italy.
[13]
Hematology Unit, University of Ferrara, Ferrara, Italy.
[14]
Hematology Division, Azienda Ospedaliera Santi Antonio e Biagio e Cesare Arrigo, Alessandria, Italy.
[15]
Unità Operativa Ematologia, Azienda Sanitaria Provinciale Trapani, Presidio Ospedaliero Castelvetrano, Trapani, Italy.
[16]
Hematology Unit and BMT Center University Hospital of Parma, Parma, Italy.
[17]
Hematology, Belcolle Hospital, Viterbo, Italy.
[18]
Haematology Unit, National Cancer Center, IRCCS Istituto Tumori "Giovanni Paolo II", Bari, Italy.
[19]
Haematology Unit, Azienda Ospedaliera S. Maria Angeli, Pordenone, Italy.
[20]
UOC Ematologia, AORN "A. Cardarelli", Napoli, Italy.
[21]
Hematology Unit, Azienda Ospedaliera Santa Maria di Terni, Terni, Italy.
[22]
Department of Cellular Therapies and Transfusion Medicine, AOU Careggi, Florence, Italy.
[23]
Division of Oncology and Hematology, ARNAS Garibaldi-Nesima, Catania, Italy.
[24]
Hematology Division, Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.
[25]
Department Hematology-Oncology, Azienda Ospedaliera Universitaria "Renato Dulbecco", Catanzaro, Italy.
[26]
Hematology Unit, Federico II University of Naples, Naples, Italy.
[27]
Hematology Department, San Bortolo Hospital, Vicenza, Italy.
[28]
Department of Clinical and Biological Sciences, Internal Medicine With Hematological Focus, AOU San Luigi, University of Turin, Turin, Italy.
[29]
UO Hematology, University Hospital Paolo Giaccone, Palermo, Italy.
[30]
Hematology Unit, Azienda Ospedaliero-Universitaria Careggi, Florence, Italy.
[31]
Hematology Unit, Azienda Ospedaliero Universitaria Ospedali Riuniti Ancona, Ancona, Italy.
[32]
Department of Translational Medicine, Hematology Unit, University of Eastern Piedmont and AOU Maggiore della Carità, Novara, Italy.
[33]
Ospedale Nuovo Santo Stefano, Prato, Italy.
[34]
Dipartimento di Patologia Umana dell'Adulto e dell'Età Evolutiva, Division of Hematology, Policlinico G. Martino, University of Messina, Messina, Italy.
[35]
Hematology Unit, ULSS 3, Dell'Angelo Hospital, Venezia-Mestre, Italy.
[36]
Department of Hematology and Stem Cell Transplantation Unit, IRCCS Casa Sollievo della Sofferenza Hospital, San Giovanni Rotondo, Italy.
[37]
Hematology Unit, Dimiccoli Hospital, Barletta, Italy.
[38]
UO di Ematologia e trapianto, Azienda Ospedaliera Cardinale G. Panico, Tricase, Italy.
[39]
Dipartimento di Scienze di laboratorio ed ematologiche, Fondazione Policlinico Universitario A. Gemelli IRCCS, Rome, Italy.;Dipartimento di Scienze Radiologiche ed Ematologiche, Sezione di Ematologia, Università Cattolica del Sacro Cuore, Rome, Italy.
[40]
Centro Ricerche Emato-Oncologiche, Institute of Hematology, Ospedale S. Maria della Misericordia, University of Perugia, Perugia, Italy.
[41]
Hematology Unit, AOU Policlinico "G. Martino", University of Messina, Messina, Italy.
[42]
Hematology Unit and BMT Center, Ospedale G. Saliceto, Piacenza, Italy.
[43]
Institute of Hematology "Seràgnoli" IRCCS Azienda Ospedaliero-Universitaria di Bologna, Bologna, Italy.;Department of Medical and Surgical Sciences, University of Bologna, Bologna, Italy.
[44]
主题词
人类(Humans);男(雄)性(Male);女(雌)性(Female);中年人(Middle Aged);老年人(Aged);体恤使用试验(Compassionate Use Trials);成年人(Adult);抗药性, 肿瘤(Drug Resistance, Neoplasm);回顾性研究(Retrospective Studies);意大利(Italy);吡唑类(Pyrazoles);蛋白激酶抑制剂(Protein Kinase Inhibitors);老年人, 80以上(Aged, 80 and over);白血病, 髓样, 慢性期(Leukemia, Myeloid, Chronic-Phase);青年人(Young Adult);白血病, 髓系, 慢性, BCR-ABL阳性(Leukemia, Myelogenous, Chronic, BCR-ABL Positive);融合蛋白质类, bcr-abl(Fusion Proteins, bcr-abl);治疗结果(Treatment Outcome);烟酰胺(Niacinamide)
DOI
10.1002/hon.70101
PMID
40344674
发布时间
2025-05-11
- 浏览1
Hematological oncology
Hematological oncology
e70101页
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