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Vutrisiran in Transthyretin Amyloidosis: A Pooled Safety Analysis of HELIOS-A and HELIOS-B.

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第一作者: Ronald M,Witteles
第一单位: Division of Cardiovascular Medicine and Stanford Amyloid Center, Stanford University School of Medicine, Stanford, California, USA. Electronic address: witteles@stanford.edu.
作者单位: Division of Cardiovascular Medicine and Stanford Amyloid Center, Stanford University School of Medicine, Stanford, California, USA. Electronic address: witteles@stanford.edu. [1] Department of Cardiology, Hospital Universitario Puerta de Hierro Majadahonda, Health Research Institute of the Puerta de Hierro Majadahonda-Segovia, Centro de Investigación Biomédica en Red Enfermedades Cardiovasculares (CIBER-CV), and Centro Nacional de Investigaciones Cardiovasculares, Madrid, Spain. [2] Department of Clinical Research and Epidemiology, Comprehensive Heart Failure Center, and the Department of Medicine I, University Hospital Würzburg, Würzburg, Germany. [3] National Amyloidosis Centre, Division of Medicine, University College London, Royal Free Hospital, London, United Kingdom. [4] Department of Clinical Immunology, Liverpool Hospital and South West Sydney Clinical Campus, UNSW Medicine and Health, Sydney, New South Wales, Australia. [5] Department of Neurosciences and Mental Health, ULS de Santa Maria, CAML, Faculty of Medicine, Centre of Studies Egas Moniz, University of Lisbon, Lisbon, Portugal. [6] Calhoun Cardiology Center, University of Connecticut School of Medicine, Farmington, Connecticut, USA. [7] Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA. [8] Department of Neurology, CHU Bicêtre, APHP, INSERM U 1195, University Paris-Saclay, Le Kremlin Bicêtre, France. [9]
DOI 10.1016/j.jacadv.2025.102066
PMID 40848527
发布时间 2025-09-26
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JACC. Advances

JACC. Advances

2025年4卷9期

102066页

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