Non-invasive liposome-mediated gene delivery can correct the ion transport defect in cystic fibrosis mutant mice.
第一作者:
E W,Alton
第一单位:
Ion Transport Laboratory, National Heart and Lung Institute, London, UK.
作者:
医学主题词
动物(Animals);碱基序列(Base Sequence);生物转运(Biological Transport);囊性纤维化(Cystic Fibrosis);囊性纤维化跨膜传导调节因子(Cystic Fibrosis Transmembrane Conductance Regulator);DNA, 互补(DNA, Complementary);基因, 报告(Genes, Reporter);人类(Humans);肠(Intestines);离子(Ions);脂质体(Liposomes);膜蛋白质类(Membrane Proteins);小鼠(Mice);小鼠, 突变型(Mice, Mutant Strains);分子序列数据(Molecular Sequence Data);雾化器和汽化器(Nebulizers and Vaporizers);寡脱氧核糖核苷酸类(Oligodeoxyribonucleotides)
DOI
10.1038/ng1093-135
PMID
7504552
发布时间
2012-11-15
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Nature genetics
135-42页
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