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Outcomes following treatment for ADA-deficient severe combined immunodeficiency: a report from the PIDTC

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第一作者: Cuvelier, Geoffrey D. E.
作者单位: Duke Univ Med Ctr [1] Microbiol Immunol & Mol Genet,Univ Calif Los Angeles [2] Mattel Childrens Hosp,Univ Calif Los Angeles [3] Benioff Childrens Hosp,Univ Calif San Francisco [4] MSK Kids,Mem Sloan Kettering Canc Ctr [5] Div Hematol Oncol & Blood & Marrow Transplant,Childrens Hosp [6] Immune Deficiency Cellular Therapy Program,NCI [7] Dana Farber Canc Inst,Boston Childrens Hosp [8] Div Pediat Blood & Marrow Transplant & Cellular T,MHlth Fairview Masonic Childrens Hosp [9] Baylor Coll Med,Texas Childrens Hosp [10] Dept Pediat,Univ Washington [11] Ctr Cell & Gene Therapy Nonmalignant Condit,Johns Hopkins All Childrens Hosp [12] Childrens Hosp Philadelphia,Univ Penn [13] Stanford Sch Med,Lucile Packard Childrens Hosp [14] Primary Childrens Hosp,Univ Utah [15] St Louis Childrens Hosp,Washington Univ [16] Coll Med,Univ Cincinnati [17] Bone Marrow Transplantat & Immune Deficiency,Childrens Hosp Atlanta [18] Childrens Canc Inst,Hackensack Univ Med Ctr [19] Methodist Childrens Hosp South Texas [20] Pediat Blood & Marrow Transplant & Cellular Thera,Michigan State Univ [21] Nemours Childrens Hlth,Thomas Jefferson Univ [22] Div Blood & Marrow Transplantat,Childrens Natl Hosp [23] Amer Family Childrens Hosp,Univ Wisconsin [24] Div Pediat Hematol Oncol BMT [25] Div Pediat Hematol & Oncol & Bone Marrow Transpla,Univ Alabama Birmingham [26] British Columbia Childrens Hosp [27] Blood & Marrow Transplant Program,Univ Michigan [28] Div Allergy & Immunol,Johns Hopkins Univ [29] Allen Inst Immunol [30] Div Pediat Hematol & Oncol,Univ Utah [31] Lab Clin Immunol & Microbiol,NIAID [32] Dept Pediat,Univ Montreal [33] CancerCare Manitoba Foundation,CancerCare Manitoba [34] Div Biostat,Med Coll Wisconsin [35] Stem Cell Transplant Serv,Boston Childrens Hosp [36] David Geffen Sch Med,Univ Calif Los Angeles [37] Div Allergy Immunol & Transplantat,NIAID [38]
发布时间 2023-02-24
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Blood: The Journal of the American Society of Hematology

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