Safety and efficacy of intravenous bimagrumab in inclusion body myositis (RESILIENT): a randomised, double-blind, placebo-controlled phase 2b trial
第一作者:
Hanna, Michael G.
作者:
Hanna, Michael G. [1]
;
Badrising, Umesh A. [2]
;
Benveniste, Olivier [3]
;
Lloyd, Thomas E. [4]
;
Needham, Merrilee [5]
;
Chinoy, Hector [6]
;
Aoki, Masashi [7]
;
Machado, Pedro M. [8]
;
Liang, Christina [9]
;
Reardon, Katrina A. [10]
;
de Visser, Marianne [11]
;
Ascherman, Dana P. [12]
;
Barohn, Richard J. [13]
;
Dimachkie, Mazen M. [14]
;
Miller, James A. L. [15]
;
Kissel, John T. [16]
;
Oskarsson, Bjoern [17]
;
Joyce, Nanette C. [18]
;
Van den Bergh, Peter [19]
;
Baets, Jonathan [20]
;
De Bleecker, Jan L. [21]
;
Karam, Chafic [22]
;
David, William S. [23]
;
Mirabella, Massimiliano [24]
;
Nations, Sharon P. [25]
;
Jung, Hans H. [26]
;
Pegoraro, Elena [27]
;
Maggi, Lorenzo [28]
;
Rodolico, Carmelo [29]
;
Filosto, Massimiliano [30]
;
Shaibani, Aziz, I [31]
;
Sivakumar, Kumaraswamy [32]
;
Goyal, Namita A. [33]
;
Mori-Yoshimura, Madoka [34]
;
Yamashita, Satoshi [35]
;
Suzuki, Naoki [36]
;
Katsuno, Masahisa [37]
;
Murata, Kenya [38]
;
Nodera, Hiroyuki [39]
;
Romano, Carla D. [40]
;
Williams, Valerie S. L. [41]
;
Vissing, John [42]
;
Auberson, Lixin Zhang ;
Wu, Min ;
de Vera, Ana ;
Papanicolaou, Dimitris A. ;
Amato, Anthony A. ;
Nishino, Ichizo
作者单位:
Newcastle Tyne Hosp NHS Fdn Trust, Dept Neurol, Newcastle Upon Tyne, Tyne & Wear, England
[1]
Tohoku Univ Hosp, Dept Neurol, Sendai, Miyagi, Japan
[2]
Univ Hosp, Dept Neurol, Zurich, Switzerland
[3]
Wakayama Med Univ Hosp, Wakayama, Japan
[4]
Univ Cattolica Sacro Cuore, Dept Neurol, Fdn Policlin Univ Agostino Gemelli, IRCCS, Rome, Italy
[5]
Neuromuscular Res Ctr, Phoenix, AZ USA
[6]
Leiden Univ, Dept Neurol, Med Ctr, Leiden, Netherlands
[7]
Natl Ctr Hosp, Natl Ctr Neurol & Psychiat, Dept Neurol, Tokyo, Japan
[8]
Sorbonne Univ, Dept Internal Med & Clin Immunol, Pitie Salpetriere Hosp, Paris, France
[9]
Johns Hopkins Univ, Sch Med, Dept Neurosci, Baltimore, MD 21205 USA
[10]
Tokushima Univ Hosp, Tokushima, Japan
[11]
Ghent Univ Hosp, Dept Neurol, Ghent, Belgium
[12]
Azienda Socio Sanit Terr Spedali Civili, Ctr Neuromuscular Dis, Unit Neurol, Brescia, Italy
[13]
Tohoku Univ, Dept Neurol, Sch Med, Sendai, Miyagi, Japan
[14]
Royal North Shore Hosp, Dept Neurol, Sydney, NSW, Australia
[15]
Fdn IRCCS Neurol Inst Carlo Besta, Neuroimmunol & Neuromuscular Dis Unit, Milan, Italy
[16]
Univ Messina, Azienda Osped Univ Policlin G Martino, Unit Neurol & Neuromuscular Disorders, Messina
[17]
Ohio State Univ, Dept Neurol, Wexner Med Ctr, Columbus, OH 43210 USA
[18]
UCL, MRC, Ctr Neuromuscular Dis, Inst Neurol, London WC1N 3BG, England
[19]
Univ Calif Irvine, Dept Neurol, Amyotroph Lateral Sclerosis & Neuromuscular Ctr, Orange, CA 92668
[20]
Univ Texas Southwestern Med Ctr Dallas, Dept Neurol, Dallas, TX 75390 USA
[21]
Nagoya Univ Hosp, Dept Neurol, Nagoya, Aichi, Japan
[22]
Univ Miami, Dept Med, Miami, FL USA
[23]
Kumamoto Univ Hosp, Dept Neurol, Kumamoto, Japan
[24]
Univ Padua, Sch Med, Dept Neurosci, Padua, Italy
[25]
Natl Ctr Neurol & Psychiat, Natl Inst Neurosci, Dept Neuromuscular Res, Tokyo, Japan
[26]
UC Davis Sch Med, Neuromuscular Res Ctr, Sacramento, CA USA
[27]
Novartis Pharmaceut, E Hanover, NJ USA
[28]
Univ Antwerp, Antwerp Univ Hosp, Neuromuscular Reference Ctr, Dept Neurol, Antwerp, Belgium
[29]
Calvary Hlth Care Bethlehem, Caulfield, Vic, Australia
[30]
Univ Copenhagen, Rigshosp, Copenhagen Neuromuscular Ctr, Copenhagen, Denmark
[31]
Murdoch Univ, Inst Immunol & Infect Dis, Fiona Stanley Hosp, Perth, WA, Australia
[32]
RTI Hlth Solut, Res Triangle Pk, NC USA
[33]
Oregon Hlth & Sci Univ, Dept Neurol, Portland, OR 97201 USA
[34]
Brigham & Womens Hosp, Dept Neurol, 75 Francis St, Boston, MA 02115 USA
[35]
Univ Louvain, Univ Hosp St Luc, Dept Neurol, Brussels, Belgium
[36]
Novartis Pharmaceut, Basel, Switzerland
[37]
Nerve & Muscle Ctr Texas, Houston, TX USA
[38]
Univ Manchester, Manchester Univ NHS Fdn Trust, Manchester Acad Hlth Sci Ctr, Natl Inst Hlth Res
[39]
Massachusetts Gen Hosp, Dept Neurol, Neuromuscular Diagnost Ctr & Electromyog Lab, Boston, MA 02114
[40]
Univ Amsterdam, Acad Med Ctr, Dept Neurol, Amsterdam, Netherlands
[41]
Univ Kansas, Med Ctr, Dept Neurol, Kansas City, KS 66103 USA
[42]
发布时间
2020-07-29
- 浏览3
Lancet Neurology
Lancet Neurology
834-844页
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