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Safety and efficacy of intravenous bimagrumab in inclusion body myositis (RESILIENT): a randomised, double-blind, placebo-controlled phase 2b trial

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第一作者: Hanna, Michael G.
作者单位: Newcastle Tyne Hosp NHS Fdn Trust, Dept Neurol, Newcastle Upon Tyne, Tyne & Wear, England [1] Tohoku Univ Hosp, Dept Neurol, Sendai, Miyagi, Japan [2] Univ Hosp, Dept Neurol, Zurich, Switzerland [3] Wakayama Med Univ Hosp, Wakayama, Japan [4] Univ Cattolica Sacro Cuore, Dept Neurol, Fdn Policlin Univ Agostino Gemelli, IRCCS, Rome, Italy [5] Neuromuscular Res Ctr, Phoenix, AZ USA [6] Leiden Univ, Dept Neurol, Med Ctr, Leiden, Netherlands [7] Natl Ctr Hosp, Natl Ctr Neurol & Psychiat, Dept Neurol, Tokyo, Japan [8] Sorbonne Univ, Dept Internal Med & Clin Immunol, Pitie Salpetriere Hosp, Paris, France [9] Johns Hopkins Univ, Sch Med, Dept Neurosci, Baltimore, MD 21205 USA [10] Tokushima Univ Hosp, Tokushima, Japan [11] Ghent Univ Hosp, Dept Neurol, Ghent, Belgium [12] Azienda Socio Sanit Terr Spedali Civili, Ctr Neuromuscular Dis, Unit Neurol, Brescia, Italy [13] Tohoku Univ, Dept Neurol, Sch Med, Sendai, Miyagi, Japan [14] Royal North Shore Hosp, Dept Neurol, Sydney, NSW, Australia [15] Fdn IRCCS Neurol Inst Carlo Besta, Neuroimmunol & Neuromuscular Dis Unit, Milan, Italy [16] Univ Messina, Azienda Osped Univ Policlin G Martino, Unit Neurol & Neuromuscular Disorders, Messina [17] Ohio State Univ, Dept Neurol, Wexner Med Ctr, Columbus, OH 43210 USA [18] UCL, MRC, Ctr Neuromuscular Dis, Inst Neurol, London WC1N 3BG, England [19] Univ Calif Irvine, Dept Neurol, Amyotroph Lateral Sclerosis & Neuromuscular Ctr, Orange, CA 92668 [20] Univ Texas Southwestern Med Ctr Dallas, Dept Neurol, Dallas, TX 75390 USA [21] Nagoya Univ Hosp, Dept Neurol, Nagoya, Aichi, Japan [22] Univ Miami, Dept Med, Miami, FL USA [23] Kumamoto Univ Hosp, Dept Neurol, Kumamoto, Japan [24] Univ Padua, Sch Med, Dept Neurosci, Padua, Italy [25] Natl Ctr Neurol & Psychiat, Natl Inst Neurosci, Dept Neuromuscular Res, Tokyo, Japan [26] UC Davis Sch Med, Neuromuscular Res Ctr, Sacramento, CA USA [27] Novartis Pharmaceut, E Hanover, NJ USA [28] Univ Antwerp, Antwerp Univ Hosp, Neuromuscular Reference Ctr, Dept Neurol, Antwerp, Belgium [29] Calvary Hlth Care Bethlehem, Caulfield, Vic, Australia [30] Univ Copenhagen, Rigshosp, Copenhagen Neuromuscular Ctr, Copenhagen, Denmark [31] Murdoch Univ, Inst Immunol & Infect Dis, Fiona Stanley Hosp, Perth, WA, Australia [32] RTI Hlth Solut, Res Triangle Pk, NC USA [33] Oregon Hlth & Sci Univ, Dept Neurol, Portland, OR 97201 USA [34] Brigham & Womens Hosp, Dept Neurol, 75 Francis St, Boston, MA 02115 USA [35] Univ Louvain, Univ Hosp St Luc, Dept Neurol, Brussels, Belgium [36] Novartis Pharmaceut, Basel, Switzerland [37] Nerve & Muscle Ctr Texas, Houston, TX USA [38] Univ Manchester, Manchester Univ NHS Fdn Trust, Manchester Acad Hlth Sci Ctr, Natl Inst Hlth Res [39] Massachusetts Gen Hosp, Dept Neurol, Neuromuscular Diagnost Ctr & Electromyog Lab, Boston, MA 02114 [40] Univ Amsterdam, Acad Med Ctr, Dept Neurol, Amsterdam, Netherlands [41] Univ Kansas, Med Ctr, Dept Neurol, Kansas City, KS 66103 USA [42]
发布时间 2020-07-29
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