首页>Journal of inherited metabolic disease>Letter to the Editors: Concerning "cRIM-negative Pompe disease patients with satisfactory clinical outcomes on enzyme replacement therapy" by Al Khallaf et al
Letter to the Editors: Concerning "cRIM-negative Pompe disease patients with satisfactory clinical outcomes on enzyme replacement therapy" by Al Khallaf et al
作者单位:Genzyme Corporation, Boston, MA, United States[1]Division of Therapeutic Proteins, Center for Drug Evaluation and Research, United States Food and[2]Department of Pediatrics, Duke University, Medical Center, Durham, NC 27710, United States[3]