作者:
Turkia,H.B. [1]
;
Gonzalez,D.E. [2]
;
Barton,N.W. [3]
;
Zimran,A. [4]
;
Kabra,M. [5]
;
Lukina,E.A. [6]
;
Giraldo,P. [7]
;
Kisinovsky,I. [8]
;
Bavdekar,A. [9]
;
Dridi,M..-F.B. [10]
;
Gupta,N. [11]
;
Kishnani,P.S. [12]
;
Sureshkumar,E.K. ;
Wang,N. ;
Crombez,E. ;
Bhirangi,K. ;
Mehta,A.
作者单位:
Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER), Hospital Universitario
[1]
Malabar Institute of Medical Sciences Ltd., Calicut, India
[2]
Royal Free Hospital, University College London School of Medicine, London, United Kingdom
[3]
Duke University Medical Center, Durham, NC, United States
[4]
KEM Hospital Research Centre, Pune, India
[5]
Shaare Zedek Medical Center and Hebrew University-Hadassah Medical School, Jerusalem, Israel
[6]
All India Institute of Medical Sciences, New Delhi, India
[7]
Your Health S.A., Buenos Aires, Argentina
[8]
Shire Human Genetic Therapies, Inc., Lexington, MA, United States
[9]
Sanatorio Espa?ol, Asunción, Paraguay
[10]
La Rabta Hospital, Tunis, Tunisia
[11]
Hematology Research Center, Moscow, Russian Federation
[12]
发布时间
2019-03-16