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Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy

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第一作者: Campbell, Craig
作者单位: Univ Massachusetts, UMass, Med Sch, Worcester, MA 01655 USA [1] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA [2] Univ Iowa, Dept Pediat, Div Pediat Neurol, Carver Coll Med, Iowa City, IA 52242 USA [3] Royal Childrens Hosp, Parkville, Vic 3052, Australia [4] Katholieke Univ Leuven, Univ Hosp Leuven, B-3000 Leuven, Belgium [5] Hop La Timone, Unite Med Infantile, F-13385 Marseille, France [6] Child Neurol Ctr Northwest Florida, Gulf Breeze, FL 32561 USA [7] Karolinska Inst, Karolinska Univ Hosp, S-17176 Stockholm, Sweden [8] Childrens Hosp Westmead, Kids Neurosci, Westmead, NSW 2145, Australia [9] Bambino Gesu Childrens Res Hosp, I-00146 Rome, Italy [10] Univ Calif Davis Hlth, Sacramento, CA 95817 USA [11] Univ Duisburg Essen, Univ Hosp Essen, Dept Pediat Neurol, D-45122 Essen, Germany [12] British Columbia Childrens Hosp, Div Neurol, Vancouver, BC V6H 3N1, Canada [13] Univ Calgary, Alberta Childrens Hosp, Dept Pediat, Div Pediat Neurol, Calgary, AB T3B 6A8, Canada [14] Hop Hotel Dieu, Reference Ctr Neuromuscular Disorders AOC, F-44000 Nantes, France [15] Univ Milan, IRCCS Fdn Ca Granda Osped Maggiore Policlin, Dino Ferrari Ctr, Dept Pathophysiol & [16] Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA [17] UCL, NIHR Great Ormond St Hosp Biomed Res Ctr, London WC1N 1EH, England [18] Gothenburg Univ, Queen Silvia Childrens Hosp, S-41685 Gothenburg, Sweden [19] Univ Kansas, Med Ctr, Kansas City, KS 66160 USA [20] Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA [21] Hosp Univ & Politecn La Fe, CIBERER, Valencia 46026, Spain [22] Catholic Univ, Dept Pediat Neurol, I-00168 Rome, Italy [23] Nationwide Childrens Hosp, Columbus, OH 43205 USA [24] Harvard Univ, Harvard TH Chan Sch Publ Hlth, Boston, MA 02115 USA [25] PTC Therapeut Inc, South Plainfield, NJ 07080 USA [26] Western Univ, Schulich Sch Med & Dent, London, ON N6A 5C1, Canada [27] Univ Freiburg, Med Ctr, Dept Neuropediat & Muscle Disorders, D-79110 Freiburg, Germany [28] Tel Aviv Univ, Schneider Childrens Med Ctr, IL-6997801 Tel Aviv, Israel [29] Stanford Univ, Dept Neurol & Neurol Sci, Med Ctr, Stanford, CA 94305 USA [30]
发布时间 2021-07-24
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Journal of comparative effectiveness research

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