Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy
第一作者:
Campbell, Craig
作者:
Campbell, Craig [1]
;
Barohn, Richard J. [2]
;
Bertini, Enrico [3]
;
Chabrol, Brigitte [4]
;
Comi, Giacomo Pietro [5]
;
Darras, Basil T. [6]
;
Finkel, Richard S. [7]
;
Flanigan, Kevin M. [8]
;
Goemans, Nathalie [9]
;
Iannaccone, Susan T. [10]
;
Jones, Kristi J. [11]
;
Kirschner, Janbernd [12]
;
Mah, Jean K. [13]
;
Mathews, Katherine D. [14]
;
McDonald, Craig M. [15]
;
Mercuri, Eugenio [16]
;
Nevo, Yoram [17]
;
Pereon, Yann [18]
;
Ben Renfroe, J. [19]
;
Ryan, Monique M. [20]
;
Sampson, Jacinda B. [21]
;
Schara, Ulrike [22]
;
Sejersen, Thomas [23]
;
Selby, Kathryn [24]
;
Tulinius, Mar [25]
;
Vilchez, Juan J. [26]
;
Voit, Thomas [27]
;
Wei, Lee-Jen [28]
;
Wong, Brenda L. [29]
;
Elfring, Gary [30]
;
Souza, Marcio ;
McIntosh, Joseph ;
Trifillis, Panayiota ;
Peltz, Stuart W. ;
Muntoni, Francesco
作者单位:
Univ Massachusetts, UMass, Med Sch, Worcester, MA 01655 USA
[1]
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
[2]
Univ Iowa, Dept Pediat, Div Pediat Neurol, Carver Coll Med, Iowa City, IA 52242 USA
[3]
Royal Childrens Hosp, Parkville, Vic 3052, Australia
[4]
Katholieke Univ Leuven, Univ Hosp Leuven, B-3000 Leuven, Belgium
[5]
Hop La Timone, Unite Med Infantile, F-13385 Marseille, France
[6]
Child Neurol Ctr Northwest Florida, Gulf Breeze, FL 32561 USA
[7]
Karolinska Inst, Karolinska Univ Hosp, S-17176 Stockholm, Sweden
[8]
Childrens Hosp Westmead, Kids Neurosci, Westmead, NSW 2145, Australia
[9]
Bambino Gesu Childrens Res Hosp, I-00146 Rome, Italy
[10]
Univ Calif Davis Hlth, Sacramento, CA 95817 USA
[11]
Univ Duisburg Essen, Univ Hosp Essen, Dept Pediat Neurol, D-45122 Essen, Germany
[12]
British Columbia Childrens Hosp, Div Neurol, Vancouver, BC V6H 3N1, Canada
[13]
Univ Calgary, Alberta Childrens Hosp, Dept Pediat, Div Pediat Neurol, Calgary, AB T3B 6A8, Canada
[14]
Hop Hotel Dieu, Reference Ctr Neuromuscular Disorders AOC, F-44000 Nantes, France
[15]
Univ Milan, IRCCS Fdn Ca Granda Osped Maggiore Policlin, Dino Ferrari Ctr, Dept Pathophysiol &
[16]
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA
[17]
UCL, NIHR Great Ormond St Hosp Biomed Res Ctr, London WC1N 1EH, England
[18]
Gothenburg Univ, Queen Silvia Childrens Hosp, S-41685 Gothenburg, Sweden
[19]
Univ Kansas, Med Ctr, Kansas City, KS 66160 USA
[20]
Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA
[21]
Hosp Univ & Politecn La Fe, CIBERER, Valencia 46026, Spain
[22]
Catholic Univ, Dept Pediat Neurol, I-00168 Rome, Italy
[23]
Nationwide Childrens Hosp, Columbus, OH 43205 USA
[24]
Harvard Univ, Harvard TH Chan Sch Publ Hlth, Boston, MA 02115 USA
[25]
PTC Therapeut Inc, South Plainfield, NJ 07080 USA
[26]
Western Univ, Schulich Sch Med & Dent, London, ON N6A 5C1, Canada
[27]
Univ Freiburg, Med Ctr, Dept Neuropediat & Muscle Disorders, D-79110 Freiburg, Germany
[28]
Tel Aviv Univ, Schneider Childrens Med Ctr, IL-6997801 Tel Aviv, Israel
[29]
Stanford Univ, Dept Neurol & Neurol Sci, Med Ctr, Stanford, CA 94305 USA
[30]
发布时间
2021-07-24
- 浏览3
Journal of comparative effectiveness research
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